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	1.	Gene Therapy for Hemophilia and Duchenne Muscular Dystrophy in China. [electronic resource] by Liu, Xionghao Liu, Mujun Wu, Lingqian Liang, Desheng Producer: 20190311 In: Human gene therapy vol. 29 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	2.	Pathogenic mutation of UBQLN2 impairs its interaction with UBXD8 and disrupts endoplasmic reticulum-associated protein degradation. [electronic resource] by Xia, Yuxing Yan, Linda H Huang, Bo Liu, Mujun Liu, Xionghao Huang, Cao Producer: 20140515 In: Journal of neurochemistry vol. 129 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	3.	ssODN-Mediated In-Frame Deletion with CRISPR/Cas9 Restores FVIII Function in Hemophilia A-Patient-Derived iPSCs and ECs. [electronic resource] by Hu, Zhiqing Zhou, Miaojin Wu, Yong Li, Zhuo Liu, Xionghao Wu, Lingqian Liang, Desheng Publication details: Molecular therapy. Nucleic acids Sep 2019 In: Molecular therapy. Nucleic acids vol. 17 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	4.	Pathogenic Ubqln2 gains toxic properties to induce neuron death. [electronic resource] by Wu, Qinxue Liu, Mujun Huang, Cao Liu, Xionghao Huang, Bo Li, Niansheng Zhou, Hongxia Xia, Xu-Gang Producer: 20151201 In: Acta neuropathologica vol. 129 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	5.	Expression of ALS-linked TDP-43 mutant in astrocytes causes non-cell-autonomous motor neuron death in rats. [electronic resource] by Tong, Jianbin Huang, Cao Bi, Fangfang Wu, Qinxue Huang, Bo Liu, Xionghao Li, Fang Zhou, Hongxia Xia, Xu-Gang Producer: 20130906 In: The EMBO journal vol. 32 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	6.	Tissue specific expression of suicide genes delivered by nanoparticles inhibits gastric carcinoma growth. [electronic resource] by Liu, Ting Zhang, Guiying Chen, Yong-Heng Chen, Yuxiang Liu, Xionghao Peng, Jie Xu, Mei Hua Yuan, Jian Wei Producer: 20070524 In: Cancer biology & therapy vol. 5 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	7.	Nonviral gene targeting at rDNA locus of human mesenchymal stem cells. [electronic resource] by Hu, Youjin Liu, Xionghao Long, Panpan Xiao, Di Cun, Jintao Li, Zhuo Xue, Jinfeng Wu, Yong Luo, Sha Wu, Lingqian Liang, Desheng Producer: 20131204 In: BioMed research international vol. 2013 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	8.	Enhanced tumor growth inhibition by mesenchymal stem cells derived from iPSCs with targeted integration of interleukin24 into rDNA loci. [electronic resource] by Liu, Bo Chen, Fei Wu, Yong Wang, Xiaolin Feng, Mai Li, Zhuo Zhou, Miaojin Wang, Yanchi Wu, Lingqian Liu, Xionghao Liang, Desheng Producer: 20180425 In: Oncotarget vol. 8 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	9.	Ectopic expression of factor VIII in MSCs and hepatocytes derived from rDNA targeted hESCs. [electronic resource] by Sun, Qianru Liu, Xionghao Wu, Yong Niu, Wenbin Long, Panpan Liu, Jing Lei, Ming Hu, Youjin Wu, Lingqian Li, Zhuo Liang, Desheng Producer: 20191202 In: Clinica chimica acta; international journal of clinical chemistry vol. 495 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	10.	Restoration of SMN expression in mesenchymal stem cells derived from gene-targeted patient-specific iPSCs. [electronic resource] by Feng, Mai Liu, Cong Xia, Yan Liu, Bo Zhou, Miaojin Li, Zhuo Sun, Qianru Hu, Zhiqing Wang, Yanchi Wu, Lingqian Liu, Xionghao Liang, Desheng Producer: 20180815 In: Journal of molecular histology vol. 49 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	11.	Paired CRISPR/Cas9 Nickases Mediate Efficient Site-Specific Integration of [electronic resource] by Wang, Yanchi Zhao, Junya Duan, Nannan Liu, Wei Zhang, Yuxuan Zhou, Miaojin Hu, Zhiqing Feng, Mai Liu, Xionghao Wu, Lingqian Li, Zhuo Liang, Desheng Producer: 20190128 In: International journal of molecular sciences vol. 19 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	12.	A non-viral vector for potential DMD gene therapy study by targeting a minidystrophin-GFP fusion gene into the hrDNA locus. [electronic resource] by Yang, Junlin Liu, Xionghao Yu, Jiaoling Sheng, Liang Shi, Yan Li, Zhuo Hu, Youjin Xue, Jinfeng Wu, Lingqian Liang, Yu Xia, Jiahui Liang, Desheng Producer: 20100329 In: Acta biochimica et biophysica Sinica vol. 41 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	13.	Seamless Genetic Conversion of SMN2 to SMN1 via CRISPR/Cpf1 and Single-Stranded Oligodeoxynucleotides in Spinal Muscular Atrophy Patient-Specific Induced Pluripotent Stem Cells. [electronic resource] by Zhou, Miaojin Hu, Zhiqing Qiu, Liyan Zhou, Tao Feng, Mai Hu, Qian Zeng, Baitao Li, Zhuo Sun, Qianru Wu, Yong Liu, Xionghao Wu, Lingqian Liang, Desheng Producer: 20191010 In: Human gene therapy vol. 29 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	14.	Generation of reporter hESCs by targeting EGFP at the CD144 locus to facilitate the endothelial differentiation. [electronic resource] by Hu, Zhiqing Wu, Yong Zhou, Miaojin Wang, Xiaolin Pang, Jialun Li, Zhuo Feng, Mai Wang, Yanchi Hu, Qian Zhao, Junya Liu, Xionghao Wu, Lingqian Liang, Desheng Producer: 20181011 In: Development, growth & differentiation vol. 60 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	15.	Targeting of the human coagulation factor IX gene at rDNA locus of human embryonic stem cells. [electronic resource] by Liu, Xionghao Wu, Yong Li, Zhuo Yang, Junlin Xue, Jinfeng Hu, Youjin Feng, Mai Niu, Wenbin Yang, Qiurui Lei, Ming Xia, Jiahui Wu, Lingqian Liang, Desheng Producer: 20130108 In: PloS one vol. 7 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	16.	Targeting of the human F8 at the multicopy rDNA locus in Hemophilia A patient-derived iPSCs using TALENickases. [electronic resource] by Pang, Jialun Wu, Yong Li, Zhuo Hu, Zhiqing Wang, Xiaolin Hu, Xuyun Wang, Xiaoyan Liu, Xionghao Zhou, Miaojin Liu, Bo Wang, Yanchi Feng, Mai Liang, Desheng Producer: 20160808 In: Biochemical and biophysical research communications vol. 472 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)
	17.	Mesenchymal stem cells derived from iPSCs expressing interleukin-24 inhibit the growth of melanoma in the tumor-bearing mouse model. [electronic resource] by Wu, Zheng Liu, Wei Wang, Zujia Zeng, Baitao Peng, Guangnan Niu, Hongyan Chen, Linlin Liu, Cong Hu, Qian Zhang, Yuxuan Pan, Mengmeng Wu, Lingqian Liu, Mujun Liu, Xionghao Liang, Desheng Publication details: Cancer cell international 2020 In: Cancer cell international vol. 20 Online resources: Available from publisher's website Availability: No items available. Save to lists Add to cart (remove)