Seamless Genetic Conversion of SMN2 to SMN1 via CRISPR/Cpf1 and Single-Stranded Oligodeoxynucleotides in Spinal Muscular Atrophy Patient-Specific Induced Pluripotent Stem Cells. [electronic resource]
Producer: 20191010Description: 1252-1263 p. digitalISSN:- 1557-7422
- Base Sequence
- Cell Differentiation
- Clone Cells
- Clustered Regularly Interspaced Short Palindromic Repeats -- genetics
- Gene Conversion
- Genotype
- Humans
- Induced Pluripotent Stem Cells -- metabolism
- Male
- Motor Neurons -- metabolism
- Muscular Atrophy, Spinal -- genetics
- Oligodeoxyribonucleotides -- metabolism
- Proto-Oncogene Proteins c-myc -- metabolism
- RNA, Guide, CRISPR-Cas Systems -- metabolism
- Survival of Motor Neuron 1 Protein -- genetics
- Survival of Motor Neuron 2 Protein -- genetics
- Young Adult
No physical items for this record
Publication Type: Journal Article; Research Support, Non-U.S. Gov't
There are no comments on this title.
Log in to your account to post a comment.