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Molecular and virological evidence of viral activation from chromosomally integrated human herpesvirus 6A in a patient with X-linked severe combined immunodeficiency. [electronic resource] by
- Endo, Akifumi
- Watanabe, Ken
- Ohye, Tamae
- Suzuki, Kyoko
- Matsubara, Tomoyo
- Shimizu, Norio
- Kurahashi, Hiroki
- Yoshikawa, Tetsushi
- Katano, Harutaka
- Inoue, Naoki
- Imai, Kohsuke
- Takagi, Masatoshi
- Morio, Tomohiro
- Mizutani, Shuki
Producer: 20150330
In:
Clinical infectious diseases : an official publication of the Infectious Diseases Society of America vol. 59
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164.
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Targeted genome editing in human repopulating haematopoietic stem cells. [electronic resource] by
- Genovese, Pietro
- Schiroli, Giulia
- Escobar, Giulia
- Tomaso, Tiziano Di
- Firrito, Claudia
- Calabria, Andrea
- Moi, Davide
- Mazzieri, Roberta
- Bonini, Chiara
- Holmes, Michael C
- Gregory, Philip D
- van der Burg, Mirjam
- Gentner, Bernhard
- Montini, Eugenio
- Lombardo, Angelo
- Naldini, Luigi
Producer: 20140715
In:
Nature vol. 510
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165.
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A modified γ-retrovirus vector for X-linked severe combined immunodeficiency. [electronic resource] by
- Hacein-Bey-Abina, Salima
- Pai, Sung-Yun
- Gaspar, H Bobby
- Armant, Myriam
- Berry, Charles C
- Blanche, Stephane
- Bleesing, Jack
- Blondeau, Johanna
- de Boer, Helen
- Buckland, Karen F
- Caccavelli, Laure
- Cros, Guilhem
- De Oliveira, Satiro
- Fernández, Karen S
- Guo, Dongjing
- Harris, Chad E
- Hopkins, Gregory
- Lehmann, Leslie E
- Lim, Annick
- London, Wendy B
- van der Loo, Johannes C M
- Malani, Nirav
- Male, Frances
- Malik, Punam
- Marinovic, M Angélica
- McNicol, Anne-Marie
- Moshous, Despina
- Neven, Benedicte
- Oleastro, Matías
- Picard, Capucine
- Ritz, Jerome
- Rivat, Christine
- Schambach, Axel
- Shaw, Kit L
- Sherman, Eric A
- Silberstein, Leslie E
- Six, Emmanuelle
- Touzot, Fabien
- Tsytsykova, Alla
- Xu-Bayford, Jinhua
- Baum, Christopher
- Bushman, Frederic D
- Fischer, Alain
- Kohn, Donald B
- Filipovich, Alexandra H
- Notarangelo, Luigi D
- Cavazzana, Marina
- Williams, David A
- Thrasher, Adrian J
Producer: 20141022
In:
The New England journal of medicine vol. 371
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Faster T-cell development following gene therapy compared with haploidentical HSCT in the treatment of SCID-X1. [electronic resource] by
- Touzot, Fabien
- Moshous, Despina
- Creidy, Rita
- Neven, Bénédicte
- Frange, Pierre
- Cros, Guilhem
- Caccavelli, Laure
- Blondeau, Johanna
- Magnani, Alessandra
- Luby, Jean-Marc
- Ternaux, Brigitte
- Picard, Capucine
- Blanche, Stéphane
- Fischer, Alain
- Hacein-Bey-Abina, Salima
- Cavazzana, Marina
Producer: 20150812
In:
Blood vol. 125
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Clinical characteristics and genotype-phenotype correlation in 62 patients with X-linked agammaglobulinemia. [electronic resource] by
- Lee, Pamela P W
- Chen, Tong-Xin
- Jiang, Li-Ping
- Chan, Koon-Wing
- Yang, Wanling
- Lee, Bee-Wah
- Chiang, Wen-Chin
- Chen, Xiang-Yuan
- Fok, Susanna F S
- Lee, Tsz-Leung
- Ho, Marco H K
- Yang, Xi-Qiang
- Lau, Yu-Lung
Producer: 20100614
In:
Journal of clinical immunology vol. 30
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171.
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Maternal T and B cell engraftment in two cases of X-linked severe combined immunodeficiency with IgG1 gammopathy. [electronic resource] by
- Okano, Tsubasa
- Nishikawa, Takuro
- Watanabe, Eri
- Watanabe, Takashi
- Takashima, Takehiro
- Yeh, Tzu-Wen
- Yamashita, Motoi
- Tanaka-Kubota, Mari
- Miyamoto, Satoshi
- Mitsuiki, Noriko
- Takagi, Masatoshi
- Kawano, Yoshifumi
- Mochizuki, Yoshiki
- Imai, Kohsuke
- Kanegane, Hirokazu
- Morio, Tomohiro
Producer: 20171121
In:
Clinical immunology (Orlando, Fla.) vol. 183
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173.
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Detection of T lymphocytes with a second-site mutation in skin lesions of atypical X-linked severe combined immunodeficiency mimicking Omenn syndrome. [electronic resource] by
- Wada, Taizo
- Yasui, Masahiro
- Toma, Tomoko
- Nakayama, Yuko
- Nishida, Mika
- Shimizu, Masaki
- Okajima, Michiko
- Kasahara, Yoshihito
- Koizumi, Shoichi
- Inoue, Masami
- Kawa, Keisei
- Yachie, Akihiro
Producer: 20080930
In:
Blood vol. 112
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Clinical and immunologic consequences of a somatic reversion in a patient with X-linked severe combined immunodeficiency. [electronic resource] by
- Speckmann, Carsten
- Pannicke, Ulrich
- Wiech, Elisabeth
- Schwarz, Klaus
- Fisch, Paul
- Friedrich, Wilhelm
- Niehues, Tim
- Gilmour, Kimberly
- Buiting, Karin
- Schlesier, Michael
- Eibel, Hermann
- Rohr, Jan
- Superti-Furga, Andrea
- Gross-Wieltsch, Ute
- Ehl, Stephan
Producer: 20081125
In:
Blood vol. 112
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Multiple reversions of an IL2RG mutation restore T cell function in an X-linked severe combined immunodeficiency patient. [electronic resource] by
- Kawai, Tomoki
- Saito, Megumu
- Nishikomori, Ryuta
- Yasumi, Takahiro
- Izawa, Kazushi
- Murakami, Tomohiko
- Okamoto, Shigefumi
- Mori, Yasuko
- Nakagawa, Noriko
- Imai, Kohsuke
- Nonoyama, Shigeaki
- Wada, Taizo
- Yachie, Akihiro
- Ohmori, Katsuyuki
- Nakahata, Tatsutoshi
- Heike, Toshio
Producer: 20130122
In:
Journal of clinical immunology vol. 32
Availability: No items available.
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