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161.
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Base Editor Correction of COL7A1 in Recessive Dystrophic Epidermolysis Bullosa Patient-Derived Fibroblasts and iPSCs. [electronic resource] by
- Osborn, Mark J
- Newby, Gregory A
- McElroy, Amber N
- Knipping, Friederike
- Nielsen, Sarah C
- Riddle, Megan J
- Xia, Lily
- Chen, Weili
- Eide, Cindy R
- Webber, Beau R
- Wandall, Hans H
- Dabelsteen, Sally
- Blazar, Bruce R
- Liu, David R
- Tolar, Jakub
Producer: 20200909
In:
The Journal of investigative dermatology vol. 140
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162.
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163.
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164.
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165.
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Targeted Repair of CYBB in X-CGD iPSCs Requires Retention of Intronic Sequences for Expression and Functional Correction. [electronic resource] by
- Sweeney, Colin L
- Zou, Jizhong
- Choi, Uimook
- Merling, Randall K
- Liu, Alexander
- Bodansky, Aaron
- Burkett, Sandra
- Kim, Jung-Woong
- De Ravin, Suk See
- Malech, Harry L
Producer: 20170606
In:
Molecular therapy : the journal of the American Society of Gene Therapy vol. 25
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166.
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169.
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171.
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172.
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Anaplastic Lymphoma Kinase Rearrangement in Digestive Tract Cancer: Implication for Targeted Therapy in Chinese Population. [electronic resource] by
- Ying, Jianming
- Lin, Chen
- Wu, Jian
- Guo, Lei
- Qiu, Tian
- Ling, Yun
- Shan, Ling
- Zhou, Haitao
- Zhao, Dongbing
- Wang, Jian
- Liang, Jianwei
- Zhao, Jianjun
- Jiao, Yuchen
- Lu, Ning
- Zhao, Hong
Producer: 20160628
In:
PloS one vol. 10
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173.
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High levels of AAV vector integration into CRISPR-induced DNA breaks. [electronic resource] by
- Hanlon, Killian S
- Kleinstiver, Benjamin P
- Garcia, Sara P
- Zaborowski, Mikołaj P
- Volak, Adrienn
- Spirig, Stefan E
- Muller, Alissa
- Sousa, Alexander A
- Tsai, Shengdar Q
- Bengtsson, Niclas E
- Lööv, Camilla
- Ingelsson, Martin
- Chamberlain, Jeffrey S
- Corey, David P
- Aryee, Martin J
- Joung, J Keith
- Breakefield, Xandra O
- Maguire, Casey A
- György, Bence
Producer: 20200106
In:
Nature communications vol. 10
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174.
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Genetic Correction of Induced Pluripotent Stem Cells From a Deaf Patient With MYO7A Mutation Results in Morphologic and Functional Recovery of the Derived Hair Cell-Like Cells. [electronic resource] by
- Tang, Zi-Hua
- Chen, Jia-Rong
- Zheng, Jing
- Shi, Hao-Song
- Ding, Jie
- Qian, Xiao-Dan
- Zhang, Cui
- Chen, Jian-Ling
- Wang, Cui-Cui
- Li, Liang
- Chen, Jun-Zhen
- Yin, Shan-Kai
- Huang, Tao-Sheng
- Chen, Ping
- Guan, Min-Xin
- Wang, Jin-Fu
Producer: 20160629
In:
Stem cells translational medicine vol. 5
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175.
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Rescue of premature aging defects in Cockayne syndrome stem cells by CRISPR/Cas9-mediated gene correction. [electronic resource] by
- Wang, Si
- Min, Zheying
- Ji, Qianzhao
- Geng, Lingling
- Su, Yao
- Liu, Zunpeng
- Hu, Huifang
- Wang, Lixia
- Zhang, Weiqi
- Suzuiki, Keiichiro
- Huang, Yu
- Zhang, Puyao
- Tang, Tie-Shan
- Qu, Jing
- Yu, Yang
- Liu, Guang-Hui
- Qiao, Jie
Producer: 20200922
In:
Protein & cell vol. 11
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176.
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Small-scale high-throughput sequencing-based identification of new therapeutic tools in cystic fibrosis. [electronic resource] by
- Bonini, Jennifer
- Varilh, Jessica
- Raynal, Caroline
- Thèze, Corinne
- Beyne, Emmanuelle
- Audrezet, Marie-Pierre
- Ferec, Claude
- Bienvenu, Thierry
- Girodon, Emmanuelle
- Tuffery-Giraud, Sylvie
- Des Georges, Marie
- Claustres, Mireille
- Taulan-Cadars, Magali
Producer: 20160413
In:
Genetics in medicine : official journal of the American College of Medical Genetics vol. 17
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