Nanoparticles deliver triplex-forming PNAs for site-specific genomic recombination in CD34+ human hematopoietic progenitors. [electronic resource]
Producer: 20110414Description: 172-80 p. digitalISSN:- 1525-0024
- Antigens, CD34 -- biosynthesis
- Cell Survival -- drug effects
- Cells, Cultured
- DNA -- genetics
- Gene Targeting -- methods
- Gene Transfer Techniques
- Genome
- Hematopoietic Stem Cells -- cytology
- Humans
- Lactic Acid -- pharmacology
- Nanoparticles -- administration & dosage
- Oligonucleotides -- pharmacology
- Particle Size
- Peptide Nucleic Acids -- administration & dosage
- Polyglycolic Acid -- pharmacology
- Polylactic Acid-Polyglycolic Acid Copolymer
- Receptors, CCR5 -- genetics
- Recombination, Genetic
- Targeted Gene Repair
- beta-Globins -- genetics
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Publication Type: Journal Article; Research Support, N.I.H., Extramural
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