Results
|
|
141.
|
|
|
|
142.
|
|
|
|
143.
|
Targeted genome editing in human repopulating haematopoietic stem cells. [electronic resource] by
- Genovese, Pietro
- Schiroli, Giulia
- Escobar, Giulia
- Tomaso, Tiziano Di
- Firrito, Claudia
- Calabria, Andrea
- Moi, Davide
- Mazzieri, Roberta
- Bonini, Chiara
- Holmes, Michael C
- Gregory, Philip D
- van der Burg, Mirjam
- Gentner, Bernhard
- Montini, Eugenio
- Lombardo, Angelo
- Naldini, Luigi
Producer: 20140715
In:
Nature vol. 510
Availability: No items available.
|
|
|
144.
|
Single-stranded oligonucleotide-mediated in vivo gene repair in the rd1 retina. [electronic resource] by
- Andrieu-Soler, Charlotte
- Halhal, Mounia
- Boatright, Jeffrey H
- Padove, Staci A
- Nickerson, John M
- Stodulkova, Eva
- Stewart, Rachael E
- Ciavatta, Vincent T
- Doat, Marc
- Jeanny, Jean-Claude
- de Bizemont, Therèse
- Sennlaub, Florian
- Courtois, Yves
- Behar-Cohen, Francine
Producer: 20070731
In:
Molecular vision vol. 13
Availability: No items available.
|
|
|
145.
|
|
|
|
146.
|
|
|
|
147.
|
|
|
|
148.
|
|
|
|
149.
|
|
|
|
150.
|
In utero nanoparticle delivery for site-specific genome editing. [electronic resource] by
- Ricciardi, Adele S
- Bahal, Raman
- Farrelly, James S
- Quijano, Elias
- Bianchi, Anthony H
- Luks, Valerie L
- Putman, Rachael
- López-Giráldez, Francesc
- Coşkun, Süleyman
- Song, Eric
- Liu, Yanfeng
- Hsieh, Wei-Che
- Ly, Danith H
- Stitelman, David H
- Glazer, Peter M
- Saltzman, W Mark
Producer: 20181211
In:
Nature communications vol. 9
Availability: No items available.
|
|
|
151.
|
Carbosilane dendrimers to transfect human astrocytes with small interfering RNA targeting human immunodeficiency virus. [electronic resource] by
- Jiménez, Jose Luis
- Clemente, María Isabel
- Weber, Nick D
- Sanchez, Javier
- Ortega, Paula
- de la Mata, F Javier
- Gómez, Rafael
- García, Dolores
- López-Fernández, Luis A
- Muñoz-Fernández, María Angeles
Producer: 20101220
In:
BioDrugs : clinical immunotherapeutics, biopharmaceuticals and gene therapy vol. 24
Availability: No items available.
|
|
|
152.
|
CRISPR/Cas9-Mediated Correction of the Sickle Mutation in Human CD34+ cells. [electronic resource] by
- Hoban, Megan D
- Lumaquin, Dianne
- Kuo, Caroline Y
- Romero, Zulema
- Long, Joseph
- Ho, Michelle
- Young, Courtney S
- Mojadidi, Michelle
- Fitz-Gibbon, Sorel
- Cooper, Aaron R
- Lill, Georgia R
- Urbinati, Fabrizia
- Campo-Fernandez, Beatriz
- Bjurstrom, Carmen F
- Pellegrini, Matteo
- Hollis, Roger P
- Kohn, Donald B
Producer: 20170606
In:
Molecular therapy : the journal of the American Society of Gene Therapy vol. 24
Availability: No items available.
|
|
|
153.
|
LRRK2 mutations cause mitochondrial DNA damage in iPSC-derived neural cells from Parkinson's disease patients: reversal by gene correction. [electronic resource] by
- Sanders, Laurie H
- Laganière, Josée
- Cooper, Oliver
- Mak, Sally K
- Vu, B Joseph
- Huang, Y Anne
- Paschon, David E
- Vangipuram, Malini
- Sundararajan, Ramya
- Urnov, Fyodor D
- Langston, J William
- Gregory, Philip D
- Zhang, H Steve
- Greenamyre, J Timothy
- Isacson, Ole
- Schüle, Birgitt
Producer: 20140903
In:
Neurobiology of disease vol. 62
Availability: No items available.
|
|
|
154.
|
Oligodendrocyte Death in Pelizaeus-Merzbacher Disease Is Rescued by Iron Chelation. [electronic resource] by
- Nobuta, Hiroko
- Yang, Nan
- Ng, Yi Han
- Marro, Samuele G
- Sabeur, Khalida
- Chavali, Manideep
- Stockley, John H
- Killilea, David W
- Walter, Patrick B
- Zhao, Chao
- Huie, Philip
- Goldman, Steven A
- Kriegstein, Arnold R
- Franklin, Robin J M
- Rowitch, David H
- Wernig, Marius
Producer: 20200921
In:
Cell stem cell vol. 25
Availability: No items available.
|
|
|
155.
|
|
|
|
156.
|
|
|
|
157.
|
|
|
|
158.
|
|
|
|
159.
|
Successful engraftment of gene-corrected hematopoietic stem cells in non-conditioned patients with Fanconi anemia. [electronic resource] by
- Río, Paula
- Navarro, Susana
- Wang, Wei
- Sánchez-Domínguez, Rebeca
- Pujol, Roser M
- Segovia, José C
- Bogliolo, Massimo
- Merino, Eva
- Wu, Ning
- Salgado, Rocío
- Lamana, María L
- Yañez, Rosa M
- Casado, José A
- Giménez, Yari
- Román-Rodríguez, Francisco J
- Álvarez, Lara
- Alberquilla, Omaira
- Raimbault, Anna
- Guenechea, Guillermo
- Lozano, M Luz
- Cerrato, Laura
- Hernando, Miriam
- Gálvez, Eva
- Hladun, Raquel
- Giralt, Irina
- Barquinero, Jordi
- Galy, Anne
- García de Andoín, Nagore
- López, Ricardo
- Catalá, Albert
- Schwartz, Jonathan D
- Surrallés, Jordi
- Soulier, Jean
- Schmidt, Manfred
- Díaz de Heredia, Cristina
- Sevilla, Julián
- Bueren, Juan A
Producer: 20191112
In:
Nature medicine vol. 25
Availability: No items available.
|
|
|
160.
|
Targeted gene editing restores regulated CD40L function in X-linked hyper-IgM syndrome. [electronic resource] by
- Hubbard, Nicholas
- Hagin, David
- Sommer, Karen
- Song, Yumei
- Khan, Iram
- Clough, Courtnee
- Ochs, Hans D
- Rawlings, David J
- Scharenberg, Andrew M
- Torgerson, Troy R
Producer: 20170623
In:
Blood vol. 127
Availability: No items available.
|