Seamless Genetic Conversion of SMN2 to SMN1 via CRISPR/Cpf1 and Single-Stranded Oligodeoxynucleotides in Spinal Muscular Atrophy Patient-Specific Induced Pluripotent Stem Cells. (Record no. 28231946)

MARC details
000 -LEADER
fixed length control field 01917 a2200541 4500
005 - DATE AND TIME OF LATEST TRANSACTION
control field 20250517210207.0
008 - FIXED-LENGTH DATA ELEMENTS--GENERAL INFORMATION
fixed length control field 201910s 0 0 eng d
022 ## - INTERNATIONAL STANDARD SERIAL NUMBER
International Standard Serial Number 1557-7422
024 7# - OTHER STANDARD IDENTIFIER
Standard number or code 10.1089/hum.2017.255
Source of number or code doi
040 ## - CATALOGING SOURCE
Original cataloging agency NLM
Language of cataloging eng
Transcribing agency NLM
100 1# - MAIN ENTRY--PERSONAL NAME
Personal name Zhou, Miaojin
264 #0 - PRODUCTION, PUBLICATION, DISTRIBUTION, MANUFACTURE, AND COPYRIGHT NOTICE
Date of production, publication, distribution, manufacture, or copyright notice 20191010
245 00 - TITLE STATEMENT
Title Seamless Genetic Conversion of SMN2 to SMN1 via CRISPR/Cpf1 and Single-Stranded Oligodeoxynucleotides in Spinal Muscular Atrophy Patient-Specific Induced Pluripotent Stem Cells.
Medium [electronic resource]
260 ## - PUBLICATION, DISTRIBUTION, ETC.
Name of publisher, distributor, etc. Human gene therapy
Date of publication, distribution, etc. Nov 2018
300 ## - PHYSICAL DESCRIPTION
Extent 1252-1263 p.
Other physical details digital
500 ## - GENERAL NOTE
General note Publication Type: Journal Article; Research Support, Non-U.S. Gov't
650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM
Topical term or geographic name entry element Base Sequence
650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM
Topical term or geographic name entry element Cell Differentiation
650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM
Topical term or geographic name entry element Clone Cells
650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM
Topical term or geographic name entry element Clustered Regularly Interspaced Short Palindromic Repeats
General subdivision genetics
650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM
Topical term or geographic name entry element Gene Conversion
650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM
Topical term or geographic name entry element Genotype
650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM
Topical term or geographic name entry element Humans
650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM
Topical term or geographic name entry element Induced Pluripotent Stem Cells
General subdivision metabolism
650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM
Topical term or geographic name entry element Male
650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM
Topical term or geographic name entry element Motor Neurons
General subdivision metabolism
650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM
Topical term or geographic name entry element Muscular Atrophy, Spinal
General subdivision genetics
650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM
Topical term or geographic name entry element Oligodeoxyribonucleotides
General subdivision metabolism
650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM
Topical term or geographic name entry element Proto-Oncogene Proteins c-myc
General subdivision metabolism
650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM
Topical term or geographic name entry element RNA, Guide, CRISPR-Cas Systems
General subdivision metabolism
650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM
Topical term or geographic name entry element Survival of Motor Neuron 1 Protein
General subdivision genetics
650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM
Topical term or geographic name entry element Survival of Motor Neuron 2 Protein
General subdivision genetics
650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM
Topical term or geographic name entry element Young Adult
700 1# - ADDED ENTRY--PERSONAL NAME
Personal name Hu, Zhiqing
700 1# - ADDED ENTRY--PERSONAL NAME
Personal name Qiu, Liyan
700 1# - ADDED ENTRY--PERSONAL NAME
Personal name Zhou, Tao
700 1# - ADDED ENTRY--PERSONAL NAME
Personal name Feng, Mai
700 1# - ADDED ENTRY--PERSONAL NAME
Personal name Hu, Qian
700 1# - ADDED ENTRY--PERSONAL NAME
Personal name Zeng, Baitao
700 1# - ADDED ENTRY--PERSONAL NAME
Personal name Li, Zhuo
700 1# - ADDED ENTRY--PERSONAL NAME
Personal name Sun, Qianru
700 1# - ADDED ENTRY--PERSONAL NAME
Personal name Wu, Yong
700 1# - ADDED ENTRY--PERSONAL NAME
Personal name Liu, Xionghao
700 1# - ADDED ENTRY--PERSONAL NAME
Personal name Wu, Lingqian
700 1# - ADDED ENTRY--PERSONAL NAME
Personal name Liang, Desheng
773 0# - HOST ITEM ENTRY
Title Human gene therapy
Related parts vol. 29
-- no. 11
-- p. 1252-1263
856 40 - ELECTRONIC LOCATION AND ACCESS
Uniform Resource Identifier <a href="https://doi.org/10.1089/hum.2017.255">https://doi.org/10.1089/hum.2017.255</a>
Public note Available from publisher's website

No items available.