Drug Screen Identifies Leflunomide for Treatment of Inflammatory Bowel Disease Caused by TTC7A Deficiency.

Jardine, Sasha

Drug Screen Identifies Leflunomide for Treatment of Inflammatory Bowel Disease Caused by TTC7A Deficiency. [electronic resource] - Gastroenterology 03 2020 - 1000-1015 p. digital

Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't

1528-0012

10.1053/j.gastro.2019.11.019 doi


Adaptor Proteins, Signal Transducing--metabolism
Animals
Apoptosis--drug effects
Apoptosis Regulatory Proteins--metabolism
Colon--cytology
Enzyme Inhibitors--pharmacology
Gene Knockout Techniques
Haploidy
Humans
Inflammatory Bowel Diseases--drug therapy
Leflunomide--pharmacology
Phosphorylation--drug effects
Proteins--genetics
X-Linked Inhibitor of Apoptosis Protein--metabolism