In vivo genome editing rescues photoreceptor degeneration via a Cas9/RecA-mediated homology-directed repair pathway.
Cai, Yuan
In vivo genome editing rescues photoreceptor degeneration via a Cas9/RecA-mediated homology-directed repair pathway. [electronic resource] - Science advances 04 2019 - eaav3335 p. digital
Publication Type: Journal Article; Research Support, Non-U.S. Gov't
2375-2548
10.1126/sciadv.aav3335 doi
Animals
CRISPR-Cas Systems--genetics
Cyclic Nucleotide Phosphodiesterases, Type 6--genetics
DNA Repair
Electroporation
Gene Editing--methods
Humans
Mice
Mice, Inbred C57BL
Rec A Recombinases--metabolism
Retinal Degeneration--therapy
Retinal Rod Photoreceptor Cells--metabolism
RNA, Guide, CRISPR-Cas Systems
In vivo genome editing rescues photoreceptor degeneration via a Cas9/RecA-mediated homology-directed repair pathway. [electronic resource] - Science advances 04 2019 - eaav3335 p. digital
Publication Type: Journal Article; Research Support, Non-U.S. Gov't
2375-2548
10.1126/sciadv.aav3335 doi
Animals
CRISPR-Cas Systems--genetics
Cyclic Nucleotide Phosphodiesterases, Type 6--genetics
DNA Repair
Electroporation
Gene Editing--methods
Humans
Mice
Mice, Inbred C57BL
Rec A Recombinases--metabolism
Retinal Degeneration--therapy
Retinal Rod Photoreceptor Cells--metabolism
RNA, Guide, CRISPR-Cas Systems