Hydroxyurea enhances SMN2 gene expression in spinal muscular atrophy cells.

Grzeschik, Susanna M

Hydroxyurea enhances SMN2 gene expression in spinal muscular atrophy cells. [electronic resource] - Annals of neurology Aug 2005 - 194-202 p. digital

Publication Type: Comparative Study; Journal Article; Research Support, Non-U.S. Gov't

0364-5134

10.1002/ana.20548 doi


Blotting, Western
Cyclic AMP Response Element-Binding Protein--genetics
Dose-Response Relationship, Drug
Enzyme Inhibitors--pharmacology
Gene Dosage
Gene Expression--drug effects
Gene Expression Regulation--drug effects
Humans
Hydroxyurea--pharmacology
Immunohistochemistry--methods
Lymphocytes--drug effects
Motor Neurons--drug effects
Muscular Atrophy, Spinal--classification
Nerve Tissue Proteins--genetics
RNA, Messenger--metabolism
RNA-Binding Proteins--genetics
Reverse Transcriptase Polymerase Chain Reaction--methods
SMN Complex Proteins
Survival of Motor Neuron 1 Protein
Survival of Motor Neuron 2 Protein
Time Factors