000 02497 a2200733 4500
005 20250518074500.0
264 0 _c20200820
008 202008s 0 0 eng d
022 _a1745-6215
024 7 _a10.1186/s13063-019-3767-8
_2doi
040 _aNLM
_beng
_cNLM
100 1 _aLeducq, Sophie
245 0 0 _aTopical sirolimus 0.1% for treating cutaneous microcystic lymphatic malformations in children and adults (TOPICAL): protocol for a multicenter phase 2, within-person, randomized, double-blind, vehicle-controlled clinical trial.
_h[electronic resource]
260 _bTrials
_cDec 2019
300 _a739 p.
_bdigital
500 _aPublication Type: Clinical Trial Protocol; Journal Article
650 0 4 _aAdministration, Cutaneous
650 0 4 _aAdolescent
650 0 4 _aAdult
650 0 4 _aChild
650 0 4 _aClinical Trials, Phase II as Topic
650 0 4 _aDermatologic Agents
_xadministration & dosage
650 0 4 _aDouble-Blind Method
650 0 4 _aFrance
650 0 4 _aHumans
650 0 4 _aLymphangiectasis
_xdrug therapy
650 0 4 _aLymphatic Abnormalities
_xdrug therapy
650 0 4 _aMulticenter Studies as Topic
650 0 4 _aQuality of Life
650 0 4 _aRandomized Controlled Trials as Topic
650 0 4 _aSirolimus
_xadministration & dosage
650 0 4 _aSkin Diseases
_xdrug therapy
650 0 4 _aTOR Serine-Threonine Kinases
_xmetabolism
650 0 4 _aTreatment Outcome
650 0 4 _aYoung Adult
700 1 _aCaille, Agnès
700 1 _aBarbarot, Sébastien
700 1 _aBénéton, Nathalie
700 1 _aBessis, Didier
700 1 _aBoccara, Olivia
700 1 _aBursztejn, Anne-Claire
700 1 _aChiaverini, Christine
700 1 _aDompmartin, Anne
700 1 _aDroitcourt, Catherine
700 1 _aGissot, Valérie
700 1 _aGoga, Dominique
700 1 _aGuibaud, Laurent
700 1 _aHerbreteau, Denis
700 1 _aLe Touze, Anne
700 1 _aLéauté-Labrèze, Christine
700 1 _aLorette, Gérard
700 1 _aMallet, Stéphanie
700 1 _aMartin, Ludovic
700 1 _aMazereeuw-Hautier, Juliette
700 1 _aPhan, Alice
700 1 _aPlantin, Patrice
700 1 _aQuéré, Isabelle
700 1 _aVabres, Pierre
700 1 _aBourgoin, Hélène
700 1 _aGiraudeau, Bruno
700 1 _aMaruani, Annabel
773 0 _tTrials
_gvol. 20
_gno. 1
_gp. 739
856 4 0 _uhttps://doi.org/10.1186/s13063-019-3767-8
_zAvailable from publisher's website
999 _c30431155
_d30431155