000 01055 a2200337 4500
005 20250518073004.0
264 0 _c20201013
008 202010s 0 0 eng d
022 _a2214-3602
024 7 _a10.3233/JND-190426
_2doi
040 _aNLM
_beng
_cNLM
100 1 _aSalabarria, S M
245 0 0 _aAdvancements in AAV-mediated Gene Therapy for Pompe Disease.
_h[electronic resource]
260 _bJournal of neuromuscular diseases
_c2020
300 _a15-31 p.
_bdigital
500 _aPublication Type: Journal Article; Review
650 0 4 _aAnimals
650 0 4 _aDependovirus
650 0 4 _aGenetic Therapy
650 0 4 _aGlycogen Storage Disease Type II
_xtherapy
650 0 4 _aHumans
700 1 _aNair, J
700 1 _aClement, N
700 1 _aSmith, B K
700 1 _aRaben, N
700 1 _aFuller, D D
700 1 _aByrne, B J
700 1 _aCorti, M
773 0 _tJournal of neuromuscular diseases
_gvol. 7
_gno. 1
_gp. 15-31
856 4 0 _uhttps://doi.org/10.3233/JND-190426
_zAvailable from publisher's website
999 _c30380950
_d30380950