| 000 | 01284 a2200337 4500 | ||
|---|---|---|---|
| 005 | 20250517224357.0 | ||
| 264 | 0 | _c20190415 | |
| 008 | 201904s 0 0 eng d | ||
| 022 | _a1750-1172 | ||
| 024 | 7 |
_a10.1186/s13023-018-0851-1 _2doi |
|
| 040 |
_aNLM _beng _cNLM |
||
| 100 | 1 | _aTingley, Kylie | |
| 245 | 0 | 0 |
_aUsing a meta-narrative literature review and focus groups with key stakeholders to identify perceived challenges and solutions for generating robust evidence on the effectiveness of treatments for rare diseases. _h[electronic resource] |
| 260 |
_bOrphanet journal of rare diseases _c06 2018 |
||
| 300 |
_a104 p. _bdigital |
||
| 500 | _aPublication Type: Journal Article; Research Support, Non-U.S. Gov't; Review | ||
| 650 | 0 | 4 | _aFocus Groups |
| 650 | 0 | 4 | _aHumans |
| 650 | 0 | 4 | _aRare Diseases |
| 650 | 0 | 4 | _aResearch Design |
| 700 | 1 | _aCoyle, Doug | |
| 700 | 1 | _aGraham, Ian D | |
| 700 | 1 | _aSikora, Lindsey | |
| 700 | 1 | _aChakraborty, Pranesh | |
| 700 | 1 | _aWilson, Kumanan | |
| 700 | 1 | _aMitchell, John J | |
| 700 | 1 | _aStockler-Ipsiroglu, Sylvia | |
| 700 | 1 | _aPotter, Beth K | |
| 773 | 0 |
_tOrphanet journal of rare diseases _gvol. 13 _gno. 1 _gp. 104 |
|
| 856 | 4 | 0 |
_uhttps://doi.org/10.1186/s13023-018-0851-1 _zAvailable from publisher's website |
| 999 |
_c28581007 _d28581007 |
||