000 01097 a2200265 4500
005 20250517210329.0
264 0 _c20181225
008 201812s 0 0 eng d
022 _a1488-2353
024 7 _a10.25011/cim.v41i1.29461
_2doi
040 _aNLM
_beng
_cNLM
100 1 _aSchneider, Raphael
245 0 0 _aCIM Journal Club: Gene therapy for spinal muscular atrophy Comment on Mendell et al. N Engl J Med 2017;377:1713-22.
_h[electronic resource]
260 _bClinical and investigative medicine. Medecine clinique et experimentale
_c03 2018
300 _aE31-E33 p.
_bdigital
500 _aPublication Type: Journal Article; Research Support, Non-U.S. Gov't; Comment
650 0 4 _aChild
650 0 4 _aGenetic Therapy
650 0 4 _aHumans
650 0 4 _aInfant
650 0 4 _aMuscular Atrophy, Spinal
650 0 4 _aSurvival of Motor Neuron 1 Protein
_xgenetics
773 0 _tClinical and investigative medicine. Medecine clinique et experimentale
_gvol. 41
_gno. 1
_gp. E31-E33
856 4 0 _uhttps://doi.org/10.25011/cim.v41i1.29461
_zAvailable from publisher's website
999 _c28236793
_d28236793