| 000 | 01917 a2200541 4500 | ||
|---|---|---|---|
| 005 | 20250517210207.0 | ||
| 264 | 0 | _c20191010 | |
| 008 | 201910s 0 0 eng d | ||
| 022 | _a1557-7422 | ||
| 024 | 7 |
_a10.1089/hum.2017.255 _2doi |
|
| 040 |
_aNLM _beng _cNLM |
||
| 100 | 1 | _aZhou, Miaojin | |
| 245 | 0 | 0 |
_aSeamless Genetic Conversion of SMN2 to SMN1 via CRISPR/Cpf1 and Single-Stranded Oligodeoxynucleotides in Spinal Muscular Atrophy Patient-Specific Induced Pluripotent Stem Cells. _h[electronic resource] |
| 260 |
_bHuman gene therapy _cNov 2018 |
||
| 300 |
_a1252-1263 p. _bdigital |
||
| 500 | _aPublication Type: Journal Article; Research Support, Non-U.S. Gov't | ||
| 650 | 0 | 4 | _aBase Sequence |
| 650 | 0 | 4 | _aCell Differentiation |
| 650 | 0 | 4 | _aClone Cells |
| 650 | 0 | 4 |
_aClustered Regularly Interspaced Short Palindromic Repeats _xgenetics |
| 650 | 0 | 4 | _aGene Conversion |
| 650 | 0 | 4 | _aGenotype |
| 650 | 0 | 4 | _aHumans |
| 650 | 0 | 4 |
_aInduced Pluripotent Stem Cells _xmetabolism |
| 650 | 0 | 4 | _aMale |
| 650 | 0 | 4 |
_aMotor Neurons _xmetabolism |
| 650 | 0 | 4 |
_aMuscular Atrophy, Spinal _xgenetics |
| 650 | 0 | 4 |
_aOligodeoxyribonucleotides _xmetabolism |
| 650 | 0 | 4 |
_aProto-Oncogene Proteins c-myc _xmetabolism |
| 650 | 0 | 4 |
_aRNA, Guide, CRISPR-Cas Systems _xmetabolism |
| 650 | 0 | 4 |
_aSurvival of Motor Neuron 1 Protein _xgenetics |
| 650 | 0 | 4 |
_aSurvival of Motor Neuron 2 Protein _xgenetics |
| 650 | 0 | 4 | _aYoung Adult |
| 700 | 1 | _aHu, Zhiqing | |
| 700 | 1 | _aQiu, Liyan | |
| 700 | 1 | _aZhou, Tao | |
| 700 | 1 | _aFeng, Mai | |
| 700 | 1 | _aHu, Qian | |
| 700 | 1 | _aZeng, Baitao | |
| 700 | 1 | _aLi, Zhuo | |
| 700 | 1 | _aSun, Qianru | |
| 700 | 1 | _aWu, Yong | |
| 700 | 1 | _aLiu, Xionghao | |
| 700 | 1 | _aWu, Lingqian | |
| 700 | 1 | _aLiang, Desheng | |
| 773 | 0 |
_tHuman gene therapy _gvol. 29 _gno. 11 _gp. 1252-1263 |
|
| 856 | 4 | 0 |
_uhttps://doi.org/10.1089/hum.2017.255 _zAvailable from publisher's website |
| 999 |
_c28231946 _d28231946 |
||