| 000 | 01744 a2200541 4500 | ||
|---|---|---|---|
| 005 | 20250517183923.0 | ||
| 264 | 0 | _c20171212 | |
| 008 | 201712s 0 0 eng d | ||
| 022 | _a1526-632X | ||
| 024 | 7 |
_a10.1212/WNL.0000000000004711 _2doi |
|
| 040 |
_aNLM _beng _cNLM |
||
| 100 | 1 | _aKuperus, Esther | |
| 245 | 0 | 0 |
_aLong-term benefit of enzyme replacement therapy in Pompe disease: A 5-year prospective study. _h[electronic resource] |
| 260 |
_bNeurology _cDec 2017 |
||
| 300 |
_a2365-2373 p. _bdigital |
||
| 500 | _aPublication Type: Journal Article | ||
| 650 | 0 | 4 | _aActivities of Daily Living |
| 650 | 0 | 4 | _aAdult |
| 650 | 0 | 4 | _aAged |
| 650 | 0 | 4 | _aCohort Studies |
| 650 | 0 | 4 |
_aEnzyme Replacement Therapy _xadverse effects |
| 650 | 0 | 4 | _aFemale |
| 650 | 0 | 4 | _aFollow-Up Studies |
| 650 | 0 | 4 |
_aGlycogen Storage Disease Type II _xdrug therapy |
| 650 | 0 | 4 | _aHumans |
| 650 | 0 | 4 | _aMale |
| 650 | 0 | 4 | _aMiddle Aged |
| 650 | 0 | 4 | _aMuscle Strength |
| 650 | 0 | 4 | _aMuscle Strength Dynamometer |
| 650 | 0 | 4 | _aProspective Studies |
| 650 | 0 | 4 | _aRespiratory Function Tests |
| 650 | 0 | 4 | _aTreatment Outcome |
| 650 | 0 | 4 | _aWalk Test |
| 650 | 0 | 4 | _aYoung Adult |
| 650 | 0 | 4 |
_aalpha-Glucosidases _xtherapeutic use |
| 700 | 1 | _aKruijshaar, Michelle E | |
| 700 | 1 | _aWens, Stephan C A | |
| 700 | 1 | _ade Vries, Juna M | |
| 700 | 1 | _aFavejee, Marein M | |
| 700 | 1 | _avan der Meijden, Jan C | |
| 700 | 1 | _aRizopoulos, Dimitris | |
| 700 | 1 | _aBrusse, Esther | |
| 700 | 1 | _avan Doorn, Pieter A | |
| 700 | 1 | _avan der Ploeg, Ans T | |
| 700 | 1 | _avan der Beek, Nadine A M E | |
| 773 | 0 |
_tNeurology _gvol. 89 _gno. 23 _gp. 2365-2373 |
|
| 856 | 4 | 0 |
_uhttps://doi.org/10.1212/WNL.0000000000004711 _zAvailable from publisher's website |
| 999 |
_c27768742 _d27768742 |
||