| 000 | 01478 a2200397 4500 | ||
|---|---|---|---|
| 005 | 20250517175656.0 | ||
| 264 | 0 | _c20180305 | |
| 008 | 201803s 0 0 eng d | ||
| 022 | _a1460-2083 | ||
| 024 | 7 |
_a10.1093/hmg/ddx215 _2doi |
|
| 040 |
_aNLM _beng _cNLM |
||
| 100 | 1 | _aWood, Matthew J A | |
| 245 | 0 | 0 |
_aSpinal muscular atrophy: antisense oligonucleotide therapy opens the door to an integrated therapeutic landscape. _h[electronic resource] |
| 260 |
_bHuman molecular genetics _c10 2017 |
||
| 300 |
_aR151-R159 p. _bdigital |
||
| 500 | _aPublication Type: Journal Article; Review | ||
| 650 | 0 | 4 | _aAnimals |
| 650 | 0 | 4 |
_aCentral Nervous System _xmetabolism |
| 650 | 0 | 4 | _aDisease Models, Animal |
| 650 | 0 | 4 | _aExons |
| 650 | 0 | 4 | _aHumans |
| 650 | 0 | 4 | _aMice |
| 650 | 0 | 4 |
_aMotor Neurons _xmetabolism |
| 650 | 0 | 4 |
_aMuscular Atrophy, Spinal _xgenetics |
| 650 | 0 | 4 |
_aOligodeoxyribonucleotides, Antisense _xgenetics |
| 650 | 0 | 4 |
_aOligonucleotides _xtherapeutic use |
| 650 | 0 | 4 |
_aOligonucleotides, Antisense _xadministration & dosage |
| 650 | 0 | 4 |
_aRNA, Messenger _xgenetics |
| 650 | 0 | 4 |
_aSpinal Cord _xmetabolism |
| 650 | 0 | 4 |
_aSurvival of Motor Neuron 1 Protein _xgenetics |
| 650 | 0 | 4 |
_aSurvival of Motor Neuron 2 Protein _xgenetics |
| 700 | 1 | _aTalbot, Kevin | |
| 700 | 1 | _aBowerman, Melissa | |
| 773 | 0 |
_tHuman molecular genetics _gvol. 26 _gno. R2 _gp. R151-R159 |
|
| 856 | 4 | 0 |
_uhttps://doi.org/10.1093/hmg/ddx215 _zAvailable from publisher's website |
| 999 |
_c27630970 _d27630970 |
||