| 000 | 01726 a2200505 4500 | ||
|---|---|---|---|
| 005 | 20250517163523.0 | ||
| 264 | 0 | _c20190624 | |
| 008 | 201906s 0 0 eng d | ||
| 022 | _a1557-7422 | ||
| 024 | 7 |
_a10.1089/hum.2017.062 _2doi |
|
| 040 |
_aNLM _beng _cNLM |
||
| 100 | 1 | _aPotter, Rachael A | |
| 245 | 0 | 0 |
_aSystemic Delivery of Dysferlin Overlap Vectors Provides Long-Term Gene Expression and Functional Improvement for Dysferlinopathy. _h[electronic resource] |
| 260 |
_bHuman gene therapy _c07 2018 |
||
| 300 |
_a749-762 p. _bdigital |
||
| 500 | _aPublication Type: Journal Article; Research Support, Non-U.S. Gov't | ||
| 650 | 0 | 4 | _aAnimals |
| 650 | 0 | 4 |
_aDNA, Complementary _xadministration & dosage |
| 650 | 0 | 4 |
_aDependovirus _xgenetics |
| 650 | 0 | 4 | _aDisease Models, Animal |
| 650 | 0 | 4 |
_aDysferlin _xadministration & dosage |
| 650 | 0 | 4 | _aGene Expression Regulation |
| 650 | 0 | 4 | _aGenetic Therapy |
| 650 | 0 | 4 |
_aGenetic Vectors _xtherapeutic use |
| 650 | 0 | 4 | _aHumans |
| 650 | 0 | 4 | _aMale |
| 650 | 0 | 4 | _aMice |
| 650 | 0 | 4 | _aMuscle, Skeletal |
| 650 | 0 | 4 |
_aMuscular Dystrophies, Limb-Girdle _xgenetics |
| 650 | 0 | 4 | _aMutation |
| 700 | 1 | _aGriffin, Danielle A | |
| 700 | 1 | _aSondergaard, Patricia C | |
| 700 | 1 | _aJohnson, Ryan W | |
| 700 | 1 | _aPozsgai, Eric R | |
| 700 | 1 | _aHeller, Kristin N | |
| 700 | 1 | _aPeterson, Ellyn L | |
| 700 | 1 | _aLehtimäki, Kimmo K | |
| 700 | 1 | _aWindish, Hillarie P | |
| 700 | 1 | _aMittal, Plavi J | |
| 700 | 1 | _aAlbrecht, Douglas E | |
| 700 | 1 | _aMendell, Jerry R | |
| 700 | 1 | _aRodino-Klapac, Louise R | |
| 773 | 0 |
_tHuman gene therapy _gvol. 29 _gno. 7 _gp. 749-762 |
|
| 856 | 4 | 0 |
_uhttps://doi.org/10.1089/hum.2017.062 _zAvailable from publisher's website |
| 999 |
_c27367927 _d27367927 |
||