000			02421 a2200721 4500
005			20250517155332.0
264		0	_c20180423
008			201804s 0 0 eng d
022			_a1525-0024
024	7		_a10.1016/j.ymthe.2017.05.004 _2doi
040			_aNLM _beng _cNLM
100	1		_aBeltran, William A
245	0	0	_aOptimization of Retinal Gene Therapy for X-Linked Retinitis Pigmentosa Due to RPGR Mutations. _h[electronic resource]
260			_bMolecular therapy : the journal of the American Society of Gene Therapy _c08 2017
300			_a1866-1880 p. _bdigital
500			_aPublication Type: Journal Article; Research Support, Non-U.S. Gov't; Research Support, N.I.H., Extramural
650	0	4	_aAnimals
650	0	4	_aCarrier Proteins _xgenetics
650	0	4	_aDependovirus _xgenetics
650	0	4	_aDisease Models, Animal
650	0	4	_aDogs
650	0	4	_aEye Proteins _xgenetics
650	0	4	_aG-Protein-Coupled Receptor Kinase 1 _xgenetics
650	0	4	_aGene Expression
650	0	4	_aGene Order
650	0	4	_aGenes, Reporter
650	0	4	_aGenes, X-Linked
650	0	4	_aGenetic Therapy
650	0	4	_aGenetic Vectors _xgenetics
650	0	4	_aHumans
650	0	4	_aMutation
650	0	4	_aPhenotype
650	0	4	_aPhotoreceptor Cells, Vertebrate _xmetabolism
650	0	4	_aPrimates
650	0	4	_aPromoter Regions, Genetic
650	0	4	_aRetina _xmetabolism
650	0	4	_aRetinitis Pigmentosa _xdiagnosis
650	0	4	_aTransduction, Genetic
650	0	4	_aTransgenes
650	0	4	_aVision Tests
700	1		_aCideciyan, Artur V
700	1		_aBoye, Shannon E
700	1		_aYe, Guo-Jie
700	1		_aIwabe, Simone
700	1		_aDufour, Valerie L
700	1		_aMarinho, Luis Felipe
700	1		_aSwider, Malgorzata
700	1		_aKosyk, Mychajlo S
700	1		_aSha, Jin
700	1		_aBoye, Sanford L
700	1		_aPeterson, James J
700	1		_aWitherspoon, C Douglas
700	1		_aAlexander, John J
700	1		_aYing, Gui-Shuang
700	1		_aShearman, Mark S
700	1		_aChulay, Jeffrey D
700	1		_aHauswirth, William W
700	1		_aGamlin, Paul D
700	1		_aJacobson, Samuel G
700	1		_aAguirre, Gustavo D
773	0		_tMolecular therapy : the journal of the American Society of Gene Therapy _gvol. 25 _gno. 8 _gp. 1866-1880
856	4	0	_uhttps://doi.org/10.1016/j.ymthe.2017.05.004 _zAvailable from publisher's website
999			_c27231181 _d27231181