000 01018 a2200265 4500
005 20250517153328.0
008 ####s 0 0 eng d
022 _a2329-0501
024 7 _a10.1016/j.omtm.2017.04.007
_2doi
040 _aNLM
_beng
_cNLM
100 1 _aGadalla, Kamal K E
245 0 0 _aDevelopment of a Novel AAV Gene Therapy Cassette with Improved Safety Features and Efficacy in a Mouse Model of Rett Syndrome.
_h[electronic resource]
260 _bMolecular therapy. Methods & clinical development
_cJun 2017
300 _a180-190 p.
_bdigital
500 _aPublication Type: Journal Article
700 1 _aVudhironarit, Thishnapha
700 1 _aHector, Ralph D
700 1 _aSinnett, Sarah
700 1 _aBahey, Noha G
700 1 _aBailey, Mark E S
700 1 _aGray, Steven J
700 1 _aCobb, Stuart R
773 0 _tMolecular therapy. Methods & clinical development
_gvol. 5
_gp. 180-190
856 4 0 _uhttps://doi.org/10.1016/j.omtm.2017.04.007
_zAvailable from publisher's website
999 _c27166334
_d27166334