000 01581 a2200433 4500
005 20250517124414.0
264 0 _c20180315
008 201803s 0 0 eng d
022 _a2214-3599
024 7 _a10.3233/JND-159900
_2doi
040 _aNLM
_beng
_cNLM
100 1 _aArgov, Zohar
245 0 0 _aAceneuramic Acid Extended Release Administration Maintains Upper Limb Muscle Strength in a 48-week Study of Subjects with GNE Myopathy: Results from a Phase 2, Randomized, Controlled Study.
_h[electronic resource]
260 _bJournal of neuromuscular diseases
_c03 2016
300 _a49-66 p.
_bdigital
500 _aPublication Type: Clinical Trial, Phase II; Journal Article; Multicenter Study; Randomized Controlled Trial; Research Support, Non-U.S. Gov't
650 0 4 _aAdolescent
650 0 4 _aAdult
650 0 4 _aDistal Myopathies
_xdrug therapy
650 0 4 _aDouble-Blind Method
650 0 4 _aFemale
650 0 4 _aHumans
650 0 4 _aMale
650 0 4 _aMiddle Aged
650 0 4 _aN-Acetylneuraminic Acid
_xadministration & dosage
650 0 4 _aOutcome Assessment, Health Care
650 0 4 _aYoung Adult
700 1 _aCaraco, Yoseph
700 1 _aLau, Heather
700 1 _aPestronk, Alan
700 1 _aShieh, Perry B
700 1 _aSkrinar, Alison
700 1 _aKoutsoukos, Tony
700 1 _aAhmed, Ruhi
700 1 _aMartinisi, Julia
700 1 _aKakkis, Emil
773 0 _tJournal of neuromuscular diseases
_gvol. 3
_gno. 1
_gp. 49-66
856 4 0 _uhttps://doi.org/10.3233/JND-159900
_zAvailable from publisher's website
999 _c26611020
_d26611020