000			01984 a2200553 4500
005			20250517095159.0
264		0	_c20170606
008			201706s 0 0 eng d
022			_a1525-0024
024	7		_a10.1038/mt.2016.97 _2doi
040			_aNLM _beng _cNLM
100	1		_aGao, Yuanzheng
245	0	0	_aGenome Therapy of Myotonic Dystrophy Type 1 iPS Cells for Development of Autologous Stem Cell Therapy. _h[electronic resource]
260			_bMolecular therapy : the journal of the American Society of Gene Therapy _c08 2016
300			_a1378-87 p. _bdigital
500			_aPublication Type: Journal Article; Research Support, Non-U.S. Gov't; Research Support, N.I.H., Extramural
650	0	4	_aAnimals
650	0	4	_aCell Differentiation
650	0	4	_aCell Nucleus _xmetabolism
650	0	4	_aCell Transformation, Neoplastic _xgenetics
650	0	4	_aDisease Models, Animal
650	0	4	_aGene Targeting
650	0	4	_aGenetic Loci
650	0	4	_aGenetic Therapy
650	0	4	_aHumans
650	0	4	_aInduced Pluripotent Stem Cells _xcytology
650	0	4	_aMice
650	0	4	_aMyocytes, Cardiac _xcytology
650	0	4	_aMyotonic Dystrophy _xgenetics
650	0	4	_aMyotonin-Protein Kinase _xgenetics
650	0	4	_aPoly A
650	0	4	_aProtein Binding
650	0	4	_aRNA Splicing
650	0	4	_aStem Cell Transplantation
650	0	4	_aTeratoma _xgenetics
650	0	4	_aTranscription Activator-Like Effector Nucleases
650	0	4	_aTransplantation, Autologous
650	0	4	_aTrinucleotide Repeats
700	1		_aGuo, Xiuming
700	1		_aSantostefano, Katherine
700	1		_aWang, Yanlin
700	1		_aReid, Tammy
700	1		_aZeng, Desmond
700	1		_aTerada, Naohiro
700	1		_aAshizawa, Tetsuo
700	1		_aXia, Guangbin
773	0		_tMolecular therapy : the journal of the American Society of Gene Therapy _gvol. 24 _gno. 8 _gp. 1378-87
856	4	0	_uhttps://doi.org/10.1038/mt.2016.97 _zAvailable from publisher's website
999			_c26042266 _d26042266