000 01217 a2200325 4500
005 20250517061250.0
264 0 _c20151030
008 201510s 0 0 eng d
022 _a1533-4406
024 7 _a10.1056/NEJMc1510466
_2doi
040 _aNLM
_beng
_cNLM
100 1 _aWainwright, Claire E
245 0 0 _aLumacaftor-Ivacaftor in Patients with Cystic Fibrosis Homozygous for Phe508del CFTR.
_h[electronic resource]
260 _bThe New England journal of medicine
_c10 2015
300 _a1783-4 p.
_bdigital
500 _aPublication Type: Letter; Comment
650 0 4 _aAminophenols
_xadministration & dosage
650 0 4 _aAminopyridines
_xadministration & dosage
650 0 4 _aBenzodioxoles
_xadministration & dosage
650 0 4 _aCystic Fibrosis
_xdrug therapy
650 0 4 _aCystic Fibrosis Transmembrane Conductance Regulator
_xgenetics
650 0 4 _aFemale
650 0 4 _aHumans
650 0 4 _aMale
650 0 4 _aQuinolones
_xadministration & dosage
700 1 _aElborn, J Stuart
700 1 _aRamsey, Bonnie W
773 0 _tThe New England journal of medicine
_gvol. 373
_gno. 18
_gp. 1783-4
856 4 0 _uhttps://doi.org/10.1056/NEJMc1510466
_zAvailable from publisher's website
999 _c25395607
_d25395607