000 01808 a2200505 4500
005 20250516231804.0
264 0 _c20151013
008 201510s 0 0 eng d
022 _a1875-5631
024 7 _a10.2174/1566523214666140825154158
_2doi
040 _aNLM
_beng
_cNLM
100 1 _aBahal, Raman
245 0 0 _aSingle-stranded γPNAs for in vivo site-specific genome editing via Watson-Crick recognition.
_h[electronic resource]
260 _bCurrent gene therapy
_c2014
300 _a331-42 p.
_bdigital
500 _aPublication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't; Research Support, U.S. Gov't, Non-P.H.S.
650 0 4 _aAnimals
650 0 4 _aBone Marrow
_xmetabolism
650 0 4 _aDNA
_xadministration & dosage
650 0 4 _aGene Targeting
650 0 4 _aGreen Fluorescent Proteins
_xgenetics
650 0 4 _aHigh-Throughput Nucleotide Sequencing
650 0 4 _aHumans
650 0 4 _aLactic Acid
650 0 4 _aMice
650 0 4 _aMice, Transgenic
650 0 4 _aNanoparticles
_xadministration & dosage
650 0 4 _aPeptide Nucleic Acids
_xadministration & dosage
650 0 4 _aPolyglycolic Acid
650 0 4 _aPolylactic Acid-Polyglycolic Acid Copolymer
650 0 4 _aRNA Editing
650 0 4 _aTissue Donors
650 0 4 _abeta-Globins
_xgenetics
700 1 _aQuijano, Elias
700 1 _aMcNeer, Nicole A
700 1 _aLiu, Yanfeng
700 1 _aBhunia, Dinesh C
700 1 _aLopez-Giraldez, Francesco
700 1 _aFields, Rachel J
700 1 _aSaltzman, William M
700 1 _aLy, Danith H
700 1 _aGlazer, Peter M
773 0 _tCurrent gene therapy
_gvol. 14
_gno. 5
_gp. 331-42
856 4 0 _uhttps://doi.org/10.2174/1566523214666140825154158
_zAvailable from publisher's website
999 _c24146625
_d24146625