000 02651 a2200805 4500
005 20250516231324.0
264 0 _c20141211
008 201412s 0 0 eng d
022 _a1531-8249
024 7 _a10.1002/ana.24260
_2doi
040 _aNLM
_beng
_cNLM
100 1 _aSoragni, Elisabetta
245 0 0 _aEpigenetic therapy for Friedreich ataxia.
_h[electronic resource]
260 _bAnnals of neurology
_cOct 2014
300 _a489-508 p.
_bdigital
500 _aPublication Type: Clinical Trial, Phase I; Journal Article; Randomized Controlled Trial; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't
650 0 4 _aAdministration, Oral
650 0 4 _aAdolescent
650 0 4 _aAdult
650 0 4 _aAminocaproates
_xpharmacology
650 0 4 _aArea Under Curve
650 0 4 _aBenzamides
_xpharmacology
650 0 4 _aCell Differentiation
_xdrug effects
650 0 4 _aCell Line, Transformed
650 0 4 _aChromatin Immunoprecipitation
650 0 4 _aCohort Studies
650 0 4 _aCross-Sectional Studies
650 0 4 _aDNA Methylation
_xdrug effects
650 0 4 _aDose-Response Relationship, Drug
650 0 4 _aDouble-Blind Method
650 0 4 _aFemale
650 0 4 _aFriedreich Ataxia
_xdrug therapy
650 0 4 _aGene Expression Regulation
_xdrug effects
650 0 4 _aHistone Deacetylase Inhibitors
_xtherapeutic use
650 0 4 _aHumans
650 0 4 _aIron-Binding Proteins
_xgenetics
650 0 4 _aLeukocytes, Mononuclear
_xdrug effects
650 0 4 _aMale
650 0 4 _aMembrane Potentials
_xdrug effects
650 0 4 _aMiddle Aged
650 0 4 _aNerve Tissue Proteins
_xgenetics
650 0 4 _aNeurons
_xdrug effects
650 0 4 _aPluripotent Stem Cells
650 0 4 _aTrinucleotide Repeat Expansion
_xgenetics
650 0 4 _aYoung Adult
650 0 4 _aFrataxin
700 1 _aMiao, Wenyan
700 1 _aIudicello, Marco
700 1 _aJacoby, David
700 1 _aDe Mercanti, Stefania
700 1 _aClerico, Marinella
700 1 _aLongo, Filomena
700 1 _aPiga, Antonio
700 1 _aKu, Sherman
700 1 _aCampau, Erica
700 1 _aDu, Jintang
700 1 _aPenalver, Pablo
700 1 _aRai, Myriam
700 1 _aMadara, Joseph C
700 1 _aNazor, Kristopher
700 1 _aO'Connor, Melinda
700 1 _aMaximov, Anton
700 1 _aLoring, Jeanne F
700 1 _aPandolfo, Massimo
700 1 _aDurelli, Luca
700 1 _aGottesfeld, Joel M
700 1 _aRusche, James R
773 0 _tAnnals of neurology
_gvol. 76
_gno. 4
_gp. 489-508
856 4 0 _uhttps://doi.org/10.1002/ana.24260
_zAvailable from publisher's website
999 _c24132871
_d24132871