000 01821 a2200553 4500
005 20250516224803.0
264 0 _c20141211
008 201412s 0 0 eng d
022 _a1526-632X
024 7 _a10.1212/WNL.0000000000000741
_2doi
040 _aNLM
_beng
_cNLM
100 1 _aFinkel, Richard S
245 0 0 _aObservational study of spinal muscular atrophy type I and implications for clinical trials.
_h[electronic resource]
260 _bNeurology
_cAug 2014
300 _a810-7 p.
_bdigital
500 _aPublication Type: Journal Article; Multicenter Study; Observational Study; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't; Research Support, U.S. Gov't, Non-P.H.S.
650 0 4 _aCohort Studies
650 0 4 _aFemale
650 0 4 _aHumans
650 0 4 _aInfant
650 0 4 _aMale
650 0 4 _aResearch Design
650 0 4 _aSpinal Muscular Atrophies of Childhood
700 1 _aMcDermott, Michael P
700 1 _aKaufmann, Petra
700 1 _aDarras, Basil T
700 1 _aChung, Wendy K
700 1 _aSproule, Douglas M
700 1 _aKang, Peter B
700 1 _aFoley, A Reghan
700 1 _aYang, Michelle L
700 1 _aMartens, William B
700 1 _aOskoui, Maryam
700 1 _aGlanzman, Allan M
700 1 _aFlickinger, Jean
700 1 _aMontes, Jacqueline
700 1 _aDunaway, Sally
700 1 _aO'Hagen, Jessica
700 1 _aQuigley, Janet
700 1 _aRiley, Susan
700 1 _aBenton, Maryjane
700 1 _aRyan, Patricia A
700 1 _aMontgomery, Megan
700 1 _aMarra, Jonathan
700 1 _aGooch, Clifton
700 1 _aDe Vivo, Darryl C
773 0 _tNeurology
_gvol. 83
_gno. 9
_gp. 810-7
856 4 0 _uhttps://doi.org/10.1212/WNL.0000000000000741
_zAvailable from publisher's website
999 _c24059220
_d24059220