| 000 | 01438 a2200397 4500 | ||
|---|---|---|---|
| 005 | 20250516185431.0 | ||
| 264 | 0 | _c20140925 | |
| 008 | 201409s 0 0 eng d | ||
| 022 | _a1932-6203 | ||
| 024 | 7 |
_a10.1371/journal.pone.0081302 _2doi |
|
| 040 |
_aNLM _beng _cNLM |
||
| 100 | 1 | _aFinkel, Richard S | |
| 245 | 0 | 0 |
_aPhase 2a study of ataluren-mediated dystrophin production in patients with nonsense mutation Duchenne muscular dystrophy. _h[electronic resource] |
| 260 |
_bPloS one _c2013 |
||
| 300 |
_ae81302 p. _bdigital |
||
| 500 | _aPublication Type: Clinical Trial, Phase II; Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't; Research Support, U.S. Gov't, P.H.S. | ||
| 650 | 0 | 4 | _aChild |
| 650 | 0 | 4 |
_aCodon, Nonsense _xgenetics |
| 650 | 0 | 4 |
_aDystrophin _xmetabolism |
| 650 | 0 | 4 | _aHumans |
| 650 | 0 | 4 | _aMale |
| 650 | 0 | 4 |
_aMuscular Dystrophy, Duchenne _xdrug therapy |
| 650 | 0 | 4 |
_aOxadiazoles _xtherapeutic use |
| 700 | 1 | _aFlanigan, Kevin M | |
| 700 | 1 | _aWong, Brenda | |
| 700 | 1 | _aBönnemann, Carsten | |
| 700 | 1 | _aSampson, Jacinda | |
| 700 | 1 | _aSweeney, H Lee | |
| 700 | 1 | _aReha, Allen | |
| 700 | 1 | _aNorthcutt, Valerie J | |
| 700 | 1 | _aElfring, Gary | |
| 700 | 1 | _aBarth, Jay | |
| 700 | 1 | _aPeltz, Stuart W | |
| 773 | 0 |
_tPloS one _gvol. 8 _gno. 12 _gp. e81302 |
|
| 856 | 4 | 0 |
_uhttps://doi.org/10.1371/journal.pone.0081302 _zAvailable from publisher's website |
| 999 |
_c23377539 _d23377539 |
||