000 01903 a2200529 4500
005 20250516132106.0
264 0 _c20130409
008 201304s 0 0 eng d
022 _a1091-6490
024 7 _a10.1073/pnas.1218933110
_2doi
040 _aNLM
_beng
_cNLM
100 1 _aCideciyan, Artur V
245 0 0 _aHuman retinal gene therapy for Leber congenital amaurosis shows advancing retinal degeneration despite enduring visual improvement.
_h[electronic resource]
260 _bProceedings of the National Academy of Sciences of the United States of America
_cFeb 2013
300 _aE517-25 p.
_bdigital
500 _aPublication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't
650 0 4 _aAdolescent
650 0 4 _aAdult
650 0 4 _aAnimals
650 0 4 _aChild
650 0 4 _aChild, Preschool
650 0 4 _aDisease Models, Animal
650 0 4 _aDogs
650 0 4 _aGenetic Therapy
650 0 4 _aHumans
650 0 4 _aLeber Congenital Amaurosis
_xgenetics
650 0 4 _aMutation
650 0 4 _aPhotoreceptor Cells, Vertebrate
_xpathology
650 0 4 _aRetinal Degeneration
_xgenetics
650 0 4 _aTime Factors
650 0 4 _aVision, Ocular
650 0 4 _aYoung Adult
650 0 4 _acis-trans-Isomerases
_xgenetics
700 1 _aJacobson, Samuel G
700 1 _aBeltran, William A
700 1 _aSumaroka, Alexander
700 1 _aSwider, Malgorzata
700 1 _aIwabe, Simone
700 1 _aRoman, Alejandro J
700 1 _aOlivares, Melani B
700 1 _aSchwartz, Sharon B
700 1 _aKomáromy, András M
700 1 _aHauswirth, William W
700 1 _aAguirre, Gustavo D
773 0 _tProceedings of the National Academy of Sciences of the United States of America
_gvol. 110
_gno. 6
_gp. E517-25
856 4 0 _uhttps://doi.org/10.1073/pnas.1218933110
_zAvailable from publisher's website
999 _c22440096
_d22440096