000			02343 a2200697 4500
005			20250516095300.0
264		0	_c20130328
008			201303s 0 0 eng d
022			_a1525-0024
024	7		_a10.1038/mt.2012.110 _2doi
040			_aNLM _beng _cNLM
100	1		_avan Til, Niek P
245	0	0	_aCorrection of murine Rag2 severe combined immunodeficiency by lentiviral gene therapy using a codon-optimized RAG2 therapeutic transgene. _h[electronic resource]
260			_bMolecular therapy : the journal of the American Society of Gene Therapy _cOct 2012
300			_a1968-80 p. _bdigital
500			_aPublication Type: Journal Article; Research Support, Non-U.S. Gov't
650	0	4	_aAnimals
650	0	4	_aB-Lymphocytes _xmetabolism
650	0	4	_aCell Proliferation
650	0	4	_aChimerism
650	0	4	_aChromatin
650	0	4	_aCodon _xgenetics
650	0	4	_aDNA-Binding Proteins _xgenetics
650	0	4	_aFemale
650	0	4	_aGene Dosage
650	0	4	_aGene Rearrangement
650	0	4	_aGenes, T-Cell Receptor beta
650	0	4	_aGenetic Therapy _xmethods
650	0	4	_aGenetic Vectors _xgenetics
650	0	4	_aHematopoietic Stem Cells _xmetabolism
650	0	4	_aLentivirus _xgenetics
650	0	4	_aMale
650	0	4	_aMice
650	0	4	_aMice, Inbred BALB C
650	0	4	_aMice, Knockout
650	0	4	_aMice, SCID
650	0	4	_aPhenotype
650	0	4	_aPlasmids
650	0	4	_aPromoter Regions, Genetic
650	0	4	_aSequence Analysis, DNA
650	0	4	_aSevere Combined Immunodeficiency _xgenetics
650	0	4	_aSpleen _xcytology
650	0	4	_aSpleen Focus-Forming Viruses _xgenetics
650	0	4	_aT-Lymphocytes _xmetabolism
650	0	4	_aTransduction, Genetic
650	0	4	_aTransgenes
700	1		_ade Boer, Helen
700	1		_aMashamba, Nomusa
700	1		_aWabik, Agnieszka
700	1		_aHuston, Marshall
700	1		_aVisser, Trudi P
700	1		_aFontana, Elena
700	1		_aPoliani, Pietro Luigi
700	1		_aCassani, Barbara
700	1		_aZhang, Fang
700	1		_aThrasher, Adrian J
700	1		_aVilla, Anna
700	1		_aWagemaker, Gerard
773	0		_tMolecular therapy : the journal of the American Society of Gene Therapy _gvol. 20 _gno. 10 _gp. 1968-80
856	4	0	_uhttps://doi.org/10.1038/mt.2012.110 _zAvailable from publisher's website
999			_c21859679 _d21859679