000 01606 a2200493 4500
005 20250516071613.0
264 0 _c20120403
008 201204s 0 0 eng d
022 _a1750-1172
024 7 _a10.1186/1750-1172-6-86
_2doi
040 _aNLM
_beng
_cNLM
100 1 _aBouazza, Naïm
245 0 0 _aPopulation pharmacokinetics and pharmacodynamics of cysteamine in nephropathic cystinosis patients.
_h[electronic resource]
260 _bOrphanet journal of rare diseases
_cDec 2011
300 _a86 p.
_bdigital
500 _aPublication Type: Clinical Trial; Journal Article
650 0 4 _aAdolescent
650 0 4 _aAdult
650 0 4 _aBody Weight
650 0 4 _aChild
650 0 4 _aChild, Preschool
650 0 4 _aCysteamine
_xadministration & dosage
650 0 4 _aCystine
_xblood
650 0 4 _aCystinosis
_xdrug therapy
650 0 4 _aDose-Response Relationship, Drug
650 0 4 _aFanconi Syndrome
650 0 4 _aFemale
650 0 4 _aHumans
650 0 4 _aInfant
650 0 4 _aMale
650 0 4 _aNephrotic Syndrome
_xdrug therapy
650 0 4 _aRadiation-Protective Agents
_xadministration & dosage
650 0 4 _aTreatment Outcome
650 0 4 _aYoung Adult
700 1 _aTréluyer, Jean-Marc
700 1 _aOttolenghi, Chris
700 1 _aUrien, Saik
700 1 _aDeschenes, Georges
700 1 _aRicquier, Daniel
700 1 _aNiaudet, Patrick
700 1 _aChadefaux-Vekemans, Bernadette
773 0 _tOrphanet journal of rare diseases
_gvol. 6
_gp. 86
856 4 0 _uhttps://doi.org/10.1186/1750-1172-6-86
_zAvailable from publisher's website
999 _c21416108
_d21416108