000 01154 a2200325 4500
005 20250516022817.0
264 0 _c20110609
008 201106s 0 0 eng d
022 _a1557-7422
024 7 _a10.1089/hum.2011.903
_2doi
040 _aNLM
_beng
_cNLM
100 1 _aButchbach, Matthew E R
245 0 0 _aTrans-splicing, more than meets the eye: multifaceted therapeutics for spinal muscular atrophy.
_h[electronic resource]
260 _bHuman gene therapy
_cFeb 2011
300 _a121-5 p.
_bdigital
500 _aPublication Type: Comment; Journal Article
650 0 4 _aAnimals
650 0 4 _aGene Expression
650 0 4 _aGenetic Therapy
650 0 4 _aHumans
650 0 4 _aInsulin-Like Growth Factor I
_xmetabolism
650 0 4 _aMice
650 0 4 _aMice, Transgenic
650 0 4 _aMuscular Atrophy, Spinal
_xgenetics
650 0 4 _aSurvival of Motor Neuron 1 Protein
_xgenetics
650 0 4 _aSurvival of Motor Neuron 2 Protein
_xgenetics
650 0 4 _aTrans-Splicing
773 0 _tHuman gene therapy
_gvol. 22
_gno. 2
_gp. 121-5
856 4 0 _uhttps://doi.org/10.1089/hum.2011.903
_zAvailable from publisher's website
999 _c20567025
_d20567025