000			02181 a2200637 4500
005			20250516021559.0
264		0	_c20111102
008			201111s 0 0 eng d
022			_a1525-0024
024	7		_a10.1038/mt.2010.274 _2doi
040			_aNLM _beng _cNLM
100	1		_aNathwani, Amit C
245	0	0	_aLong-term safety and efficacy following systemic administration of a self-complementary AAV vector encoding human FIX pseudotyped with serotype 5 and 8 capsid proteins. _h[electronic resource]
260			_bMolecular therapy : the journal of the American Society of Gene Therapy _cMay 2011
300			_a876-85 p. _bdigital
500			_aPublication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't
650	0	4	_aAnimals
650	0	4	_aCapsid Proteins _xgenetics
650	0	4	_aDependovirus _xgenetics
650	0	4	_aFactor IX _xgenetics
650	0	4	_aGene Expression
650	0	4	_aGenetic Therapy _xmethods
650	0	4	_aGenetic Vectors
650	0	4	_aHEK293 Cells
650	0	4	_aHemophilia B _xgenetics
650	0	4	_aHumans
650	0	4	_aIn Situ Hybridization, Fluorescence
650	0	4	_aLiver _xmetabolism
650	0	4	_aMacaca
650	0	4	_aMice
700	1		_aRosales, Cecilia
700	1		_aMcIntosh, Jenny
700	1		_aRastegarlari, Ghasem
700	1		_aNathwani, Devhrut
700	1		_aRaj, Deepak
700	1		_aNawathe, Sushmita
700	1		_aWaddington, Simon N
700	1		_aBronson, Roderick
700	1		_aJackson, Scott
700	1		_aDonahue, Robert E
700	1		_aHigh, Katherine A
700	1		_aMingozzi, Federico
700	1		_aNg, Catherine Y C
700	1		_aZhou, Junfang
700	1		_aSpence, Yunyu
700	1		_aMcCarville, M Beth
700	1		_aValentine, Marc
700	1		_aAllay, James
700	1		_aColeman, John
700	1		_aSleep, Susan
700	1		_aGray, John T
700	1		_aNienhuis, Arthur W
700	1		_aDavidoff, Andrew M
773	0		_tMolecular therapy : the journal of the American Society of Gene Therapy _gvol. 19 _gno. 5 _gp. 876-85
856	4	0	_uhttps://doi.org/10.1038/mt.2010.274 _zAvailable from publisher's website
999			_c20528120 _d20528120