| 000 | 01775 a2200529 4500 | ||
|---|---|---|---|
| 005 | 20250516012920.0 | ||
| 264 | 0 | _c20110610 | |
| 008 | 201106s 0 0 eng d | ||
| 022 | _a1946-6242 | ||
| 024 | 7 |
_a10.1126/scitranslmed.3001522 _2doi |
|
| 040 |
_aNLM _beng _cNLM |
||
| 100 | 1 | _aGentner, Bernhard | |
| 245 | 0 | 0 |
_aIdentification of hematopoietic stem cell-specific miRNAs enables gene therapy of globoid cell leukodystrophy. _h[electronic resource] |
| 260 |
_bScience translational medicine _cNov 2010 |
||
| 300 |
_a58ra84 p. _bdigital |
||
| 500 | _aPublication Type: Journal Article; Research Support, Non-U.S. Gov't | ||
| 650 | 0 | 4 | _aAnimals |
| 650 | 0 | 4 | _aCell Differentiation |
| 650 | 0 | 4 | _aCell Separation |
| 650 | 0 | 4 | _aCytoprotection |
| 650 | 0 | 4 |
_aGalactosylceramidase _xmetabolism |
| 650 | 0 | 4 | _aGene Expression Regulation |
| 650 | 0 | 4 | _aGenes, Transgenic, Suicide |
| 650 | 0 | 4 | _aGenetic Therapy |
| 650 | 0 | 4 |
_aHematopoietic Stem Cells _xcytology |
| 650 | 0 | 4 | _aHumans |
| 650 | 0 | 4 |
_aLeukodystrophy, Globoid Cell _xgenetics |
| 650 | 0 | 4 | _aMice |
| 650 | 0 | 4 | _aMice, SCID |
| 650 | 0 | 4 |
_aMicroRNAs _xgenetics |
| 650 | 0 | 4 |
_aOrgan Specificity _xgenetics |
| 700 | 1 | _aVisigalli, Ilaria | |
| 700 | 1 | _aHiramatsu, Hidefumi | |
| 700 | 1 | _aLechman, Eric | |
| 700 | 1 | _aUngari, Silvia | |
| 700 | 1 | _aGiustacchini, Alice | |
| 700 | 1 | _aSchira, Giulia | |
| 700 | 1 | _aAmendola, Mario | |
| 700 | 1 | _aQuattrini, Angelo | |
| 700 | 1 | _aMartino, Sabata | |
| 700 | 1 | _aOrlacchio, Aldo | |
| 700 | 1 | _aDick, John E | |
| 700 | 1 | _aBiffi, Alessandra | |
| 700 | 1 | _aNaldini, Luigi | |
| 773 | 0 |
_tScience translational medicine _gvol. 2 _gno. 58 _gp. 58ra84 |
|
| 856 | 4 | 0 |
_uhttps://doi.org/10.1126/scitranslmed.3001522 _zAvailable from publisher's website |
| 999 |
_c20381402 _d20381402 |
||