000 01662 a2200493 4500
005 20250516003056.0
264 0 _c20110120
008 201101s 0 0 eng d
022 _a1946-6242
024 7 _a10.1126/scitranslmed.3000951
_2doi
040 _aNLM
_beng
_cNLM
100 1 _aKrahn, Martin
245 0 0 _aA naturally occurring human minidysferlin protein repairs sarcolemmal lesions in a mouse model of dysferlinopathy.
_h[electronic resource]
260 _bScience translational medicine
_cSep 2010
300 _a50ra69 p.
_bdigital
500 _aPublication Type: Journal Article; Research Support, Non-U.S. Gov't
650 0 4 _aAnimals
650 0 4 _aDependovirus
_xgenetics
650 0 4 _aDisease Models, Animal
650 0 4 _aDysferlin
650 0 4 _aGenetic Therapy
650 0 4 _aHumans
650 0 4 _aMembrane Proteins
_xgenetics
650 0 4 _aMice
650 0 4 _aMuscle Proteins
_xgenetics
650 0 4 _aMuscular Dystrophies, Limb-Girdle
_xtherapy
700 1 _aWein, Nicolas
700 1 _aBartoli, Marc
700 1 _aLostal, William
700 1 _aCourrier, Sébastien
700 1 _aBourg-Alibert, Nathalie
700 1 _aNguyen, Karine
700 1 _aVial, Christophe
700 1 _aStreichenberger, Nathalie
700 1 _aLabelle, Véronique
700 1 _aDePetris, Danielle
700 1 _aPécheux, Christophe
700 1 _aLeturcq, France
700 1 _aCau, Pierre
700 1 _aRichard, Isabelle
700 1 _aLévy, Nicolas
773 0 _tScience translational medicine
_gvol. 2
_gno. 50
_gp. 50ra69
856 4 0 _uhttps://doi.org/10.1126/scitranslmed.3000951
_zAvailable from publisher's website
999 _c20191459
_d20191459