| 000 | 01548 a2200433 4500 | ||
|---|---|---|---|
| 005 | 20250515231022.0 | ||
| 264 | 0 | _c20101223 | |
| 008 | 201012s 0 0 eng d | ||
| 022 | _a1521-2254 | ||
| 024 | 7 |
_a10.1002/jgm.1478 _2doi |
|
| 040 |
_aNLM _beng _cNLM |
||
| 100 | 1 | _aRobert-Richard, Elodie | |
| 245 | 0 | 0 |
_aModeling of congenital erythropoietic porphyria by RNA interference: a new tool for preclinical gene therapy evaluation. _h[electronic resource] |
| 260 |
_bThe journal of gene medicine _cAug 2010 |
||
| 300 |
_a637-46 p. _bdigital |
||
| 500 | _aPublication Type: Evaluation Study; Journal Article; Research Support, Non-U.S. Gov't | ||
| 650 | 0 | 4 | _aAnimals |
| 650 | 0 | 4 | _aDisease Models, Animal |
| 650 | 0 | 4 |
_aGenetic Therapy _xmethods |
| 650 | 0 | 4 |
_aHematopoietic Stem Cells _xmetabolism |
| 650 | 0 | 4 | _aHumans |
| 650 | 0 | 4 | _aK562 Cells |
| 650 | 0 | 4 |
_aLentivirus _xgenetics |
| 650 | 0 | 4 | _aMice |
| 650 | 0 | 4 |
_aPorphyria, Erythropoietic _xenzymology |
| 650 | 0 | 4 | _aRNA Interference |
| 650 | 0 | 4 |
_aUroporphyrinogen III Synthetase _xgenetics |
| 700 | 1 | _aLalanne, Magalie | |
| 700 | 1 | _aLamrissi-Garcia, Isabelle | |
| 700 | 1 | _aGuyonnet-Duperat, Véronique | |
| 700 | 1 | _aRichard, Emmanuel | |
| 700 | 1 | _aPitard, Vincent | |
| 700 | 1 | _aMazurier, Fréderic | |
| 700 | 1 | _aMoreau-Gaudry, François | |
| 700 | 1 | _aGed, Cécile | |
| 700 | 1 | _ade Verneuil, Hubert | |
| 773 | 0 |
_tThe journal of gene medicine _gvol. 12 _gno. 8 _gp. 637-46 |
|
| 856 | 4 | 0 |
_uhttps://doi.org/10.1002/jgm.1478 _zAvailable from publisher's website |
| 999 |
_c19933550 _d19933550 |
||