000 01699 a2200493 4500
005 20250515144333.0
264 0 _c20090505
008 200905s 0 0 eng d
022 _a1525-0024
024 7 _a10.1038/mt.2008.223
_2doi
040 _aNLM
_beng
_cNLM
100 1 _aNiiya, Masami
245 0 0 _aCorrection of ADAMTS13 deficiency by in utero gene transfer of lentiviral vector encoding ADAMTS13 genes.
_h[electronic resource]
260 _bMolecular therapy : the journal of the American Society of Gene Therapy
_cJan 2009
300 _a34-41 p.
_bdigital
500 _aPublication Type: Journal Article; Research Support, N.I.H., Extramural
650 0 4 _aADAM Proteins
_xdeficiency
650 0 4 _aADAMTS13 Protein
650 0 4 _aAnimals
650 0 4 _aBlotting, Western
650 0 4 _aFemale
650 0 4 _aGenetic Therapy
_xmethods
650 0 4 _aGenetic Vectors
_xgenetics
650 0 4 _aHumans
650 0 4 _aImmunoprecipitation
650 0 4 _aLentivirus
_xgenetics
650 0 4 _aMice
650 0 4 _aMice, Mutant Strains
650 0 4 _aMicroscopy, Fluorescence
650 0 4 _aPurpura, Thrombotic Thrombocytopenic
_xgenetics
650 0 4 _aUterus
700 1 _aEndo, Masayuki
700 1 _aShang, Dezhi
700 1 _aZoltick, Philip W
700 1 _aMuvarak, Nidal E
700 1 _aCao, Wenjing
700 1 _aJin, Sheng-Yu
700 1 _aSkipwith, Christopher G
700 1 _aMotto, David G
700 1 _aFlake, Alan W
700 1 _aZheng, X Long
773 0 _tMolecular therapy : the journal of the American Society of Gene Therapy
_gvol. 17
_gno. 1
_gp. 34-41
856 4 0 _uhttps://doi.org/10.1038/mt.2008.223
_zAvailable from publisher's website
999 _c18420188
_d18420188