000 01453 a2200421 4500
005 20250515132353.0
264 0 _c20090706
008 200907s 0 0 eng d
022 _a1476-5462
024 7 _a10.1038/gt.2008.138
_2doi
040 _aNLM
_beng
_cNLM
100 1 _aMarquis, J
245 0 0 _aDoxycycline-controlled splicing modulation by regulated antisense U7 snRNA expression cassettes.
_h[electronic resource]
260 _bGene therapy
_cJan 2009
300 _a70-7 p.
_bdigital
500 _aPublication Type: Journal Article; Research Support, Non-U.S. Gov't
650 0 4 _aAlternative Splicing
650 0 4 _aDoxycycline
_xpharmacology
650 0 4 _aExons
650 0 4 _aGene Expression
650 0 4 _aGene Expression Regulation
_xdrug effects
650 0 4 _aGenetic Engineering
650 0 4 _aGenetic Therapy
_xmethods
650 0 4 _aHeLa Cells
650 0 4 _aHumans
650 0 4 _aMuscular Atrophy, Spinal
_xgenetics
650 0 4 _aOligonucleotides, Antisense
_xgenetics
650 0 4 _aRNA Splicing
650 0 4 _aRNA, Small Nuclear
_xgenetics
650 0 4 _aSurvival of Motor Neuron 2 Protein
_xgenetics
650 0 4 _abeta-Globins
_xgenetics
650 0 4 _abeta-Thalassemia
_xgenetics
700 1 _aKämpfer, S S
700 1 _aAngehrn, L
700 1 _aSchümperli, D
773 0 _tGene therapy
_gvol. 16
_gno. 1
_gp. 70-7
856 4 0 _uhttps://doi.org/10.1038/gt.2008.138
_zAvailable from publisher's website
999 _c18175039
_d18175039