000 01605 a2200457 4500
005 20250515103530.0
264 0 _c20080130
008 200801s 0 0 eng d
022 _a1537-6605
024 7 _a10.1016/j.ajhg.2007.09.007
_2doi
040 _aNLM
_beng
_cNLM
100 1 _aRobert-Richard, Elodie
245 0 0 _aEffective gene therapy of mice with congenital erythropoietic porphyria is facilitated by a survival advantage of corrected erythroid cells.
_h[electronic resource]
260 _bAmerican journal of human genetics
_cJan 2008
300 _a113-24 p.
_bdigital
500 _aPublication Type: Journal Article; Research Support, Non-U.S. Gov't
650 0 4 _aAnimals
650 0 4 _aCell Survival
650 0 4 _aDisease Models, Animal
650 0 4 _aErythrocytes
650 0 4 _aFemale
650 0 4 _aGenetic Therapy
650 0 4 _aGenetic Vectors
650 0 4 _aHematopoietic Stem Cells
650 0 4 _aLentivirus
650 0 4 _aMale
650 0 4 _aMice
650 0 4 _aMice, Inbred BALB C
650 0 4 _aPorphyria, Erythropoietic
_xgenetics
650 0 4 _aUroporphyrinogen III Synthetase
_xgenetics
700 1 _aMoreau-Gaudry, François
700 1 _aLalanne, Magalie
700 1 _aLamrissi-Garcia, Isabelle
700 1 _aCario-André, Muriel
700 1 _aGuyonnet-Dupérat, Véronique
700 1 _aTaine, Laurence
700 1 _aGed, Cécile
700 1 _ade Verneuil, Hubert
773 0 _tAmerican journal of human genetics
_gvol. 82
_gno. 1
_gp. 113-24
856 4 0 _uhttps://doi.org/10.1016/j.ajhg.2007.09.007
_zAvailable from publisher's website
999 _c17689899
_d17689899