| 000 | 01604 a2200469 4500 | ||
|---|---|---|---|
| 005 | 20250515080157.0 | ||
| 264 | 0 | _c20071019 | |
| 008 | 200710s 0 0 eng d | ||
| 022 | _a1474-4422 | ||
| 024 | 7 |
_a10.1016/S1474-4422(07)70194-1 _2doi |
|
| 040 |
_aNLM _beng _cNLM |
||
| 100 | 1 | _aPatterson, Marc C | |
| 245 | 0 | 0 |
_aMiglustat for treatment of Niemann-Pick C disease: a randomised controlled study. _h[electronic resource] |
| 260 |
_bThe Lancet. Neurology _cSep 2007 |
||
| 300 |
_a765-72 p. _bdigital |
||
| 500 | _aPublication Type: Clinical Trial; Journal Article; Randomized Controlled Trial; Research Support, Non-U.S. Gov't | ||
| 650 | 0 | 4 |
_a1-Deoxynojirimycin _xanalogs & derivatives |
| 650 | 0 | 4 | _aAdolescent |
| 650 | 0 | 4 | _aAdult |
| 650 | 0 | 4 | _aAge Factors |
| 650 | 0 | 4 | _aAnalysis of Variance |
| 650 | 0 | 4 | _aChild |
| 650 | 0 | 4 | _aChild, Preschool |
| 650 | 0 | 4 | _aCohort Studies |
| 650 | 0 | 4 |
_aDeglutition _xdrug effects |
| 650 | 0 | 4 | _aDouble-Blind Method |
| 650 | 0 | 4 | _aDrug Administration Schedule |
| 650 | 0 | 4 |
_aEnzyme Inhibitors _xtherapeutic use |
| 650 | 0 | 4 | _aFemale |
| 650 | 0 | 4 | _aHumans |
| 650 | 0 | 4 | _aMale |
| 650 | 0 | 4 |
_aNiemann-Pick Disease, Type C _xdrug therapy |
| 650 | 0 | 4 | _aRetrospective Studies |
| 650 | 0 | 4 |
_aSaccades _xdrug effects |
| 650 | 0 | 4 | _aSeverity of Illness Index |
| 700 | 1 | _aVecchio, Darleen | |
| 700 | 1 | _aPrady, Helena | |
| 700 | 1 | _aAbel, Larry | |
| 700 | 1 | _aWraith, James E | |
| 773 | 0 |
_tThe Lancet. Neurology _gvol. 6 _gno. 9 _gp. 765-72 |
|
| 856 | 4 | 0 |
_uhttps://doi.org/10.1016/S1474-4422(07)70194-1 _zAvailable from publisher's website |
| 999 |
_c17220960 _d17220960 |
||