000 01563 a2200433 4500
005 20250515073441.0
264 0 _c20070803
008 200708s 0 0 eng d
022 _a1098-4275
024 7 _a10.1542/peds.2006-2156
_2doi
040 _aNLM
_beng
_cNLM
100 1 _aWraith, J Edmond
245 0 0 _aEnzyme replacement therapy in patients who have mucopolysaccharidosis I and are younger than 5 years: results of a multinational study of recombinant human alpha-L-iduronidase (laronidase).
_h[electronic resource]
260 _bPediatrics
_cJul 2007
300 _ae37-46 p.
_bdigital
500 _aPublication Type: Clinical Trial; Journal Article; Multicenter Study; Research Support, Non-U.S. Gov't
650 0 4 _aChild Development
650 0 4 _aChild, Preschool
650 0 4 _aFemale
650 0 4 _aGlycosaminoglycans
_xurine
650 0 4 _aHumans
650 0 4 _aIduronidase
_xadministration & dosage
650 0 4 _aImmunoglobulin G
_xblood
650 0 4 _aInfant
650 0 4 _aInfusions, Intravenous
650 0 4 _aLiver
_xpathology
650 0 4 _aMale
650 0 4 _aMucopolysaccharidosis I
_xdrug therapy
650 0 4 _aRecombinant Proteins
_xadministration & dosage
700 1 _aBeck, Michael
700 1 _aLane, Roderick
700 1 _avan der Ploeg, Ans
700 1 _aShapiro, Elsa
700 1 _aXue, Yong
700 1 _aKakkis, Emil D
700 1 _aGuffon, Nathalie
773 0 _tPediatrics
_gvol. 120
_gno. 1
_gp. e37-46
856 4 0 _uhttps://doi.org/10.1542/peds.2006-2156
_zAvailable from publisher's website
999 _c17142779
_d17142779