| 000 | 01534 a2200397 4500 | ||
|---|---|---|---|
| 005 | 20250515051435.0 | ||
| 264 | 0 | _c20080331 | |
| 008 | 200803s 0 0 eng d | ||
| 022 | _a1525-0024 | ||
| 024 | 7 |
_a10.1038/sj.mt.6300004 _2doi |
|
| 040 |
_aNLM _beng _cNLM |
||
| 100 | 1 | _aBroekman, M L D | |
| 245 | 0 | 0 |
_aComplete correction of enzymatic deficiency and neurochemistry in the GM1-gangliosidosis mouse brain by neonatal adeno-associated virus-mediated gene delivery. _h[electronic resource] |
| 260 |
_bMolecular therapy : the journal of the American Society of Gene Therapy _cJan 2007 |
||
| 300 |
_a30-7 p. _bdigital |
||
| 500 | _aPublication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't | ||
| 650 | 0 | 4 | _aAnimals |
| 650 | 0 | 4 | _aAnimals, Newborn |
| 650 | 0 | 4 | _aChromatography, High Pressure Liquid |
| 650 | 0 | 4 |
_aDependovirus _xgenetics |
| 650 | 0 | 4 |
_aGangliosidosis, GM1 _xenzymology |
| 650 | 0 | 4 | _aGenetic Therapy |
| 650 | 0 | 4 | _aLipid Metabolism |
| 650 | 0 | 4 |
_aLysosomes _xenzymology |
| 650 | 0 | 4 | _aMice |
| 650 | 0 | 4 | _aMice, Inbred C57BL |
| 650 | 0 | 4 | _aMice, Knockout |
| 650 | 0 | 4 |
_abeta-Galactosidase _xdeficiency |
| 700 | 1 | _aBaek, R C | |
| 700 | 1 | _aComer, L A | |
| 700 | 1 | _aFernandez, J L | |
| 700 | 1 | _aSeyfried, T N | |
| 700 | 1 | _aSena-Esteves, M | |
| 773 | 0 |
_tMolecular therapy : the journal of the American Society of Gene Therapy _gvol. 15 _gno. 1 _gp. 30-7 |
|
| 856 | 4 | 0 |
_uhttps://doi.org/10.1038/sj.mt.6300004 _zAvailable from publisher's website |
| 999 |
_c16733209 _d16733209 |
||