000 01087 a2200301 4500
005 20250514030400.0
264 0 _c20020613
008 200206s 0 0 eng d
022 _a0012-6667
024 7 _a10.2165/00003495-200262050-00002
_2doi
040 _aNLM
_beng
_cNLM
100 1 _aSchiffmann, Raphael
245 0 0 _aNew prospects for the treatment of lysosomal storage diseases.
_h[electronic resource]
260 _bDrugs
_c2002
300 _a733-42 p.
_bdigital
500 _aPublication Type: Journal Article; Research Support, U.S. Gov't, P.H.S.; Review
650 0 4 _aBone Marrow Transplantation
650 0 4 _aFabry Disease
_xtherapy
650 0 4 _aGaucher Disease
_xtherapy
650 0 4 _aGenetic Therapy
650 0 4 _aGlucosylceramidase
_xtherapeutic use
650 0 4 _aHumans
650 0 4 _aLysosomal Storage Diseases
_xtherapy
650 0 4 _aMucopolysaccharidoses
_xtherapy
700 1 _aBrady, Roscoe O
773 0 _tDrugs
_gvol. 62
_gno. 5
_gp. 733-42
856 4 0 _uhttps://doi.org/10.2165/00003495-200262050-00002
_zAvailable from publisher's website
999 _c11833750
_d11833750