000 02075 a2200625 4500
005 20250514015642.0
264 0 _c20020102
008 200201s 0 0 eng d
022 _a1464-8431
040 _aNLM
_beng
_cNLM
100 1 _aLeone, P
245 0 0 _aGlobal CNS gene transfer for a childhood neurogenetic enzyme deficiency: Canavan disease.
_h[electronic resource]
260 _bCurrent opinion in molecular therapeutics
_cAug 1999
300 _a487-92 p.
_bdigital
500 _aPublication Type: Journal Article; Review
650 0 4 _aAcetates
_xtherapeutic use
650 0 4 _aAcetazolamide
_xtherapeutic use
650 0 4 _aAmidohydrolases
_xdeficiency
650 0 4 _aAnimals
650 0 4 _aAspartic Acid
_xanalogs & derivatives
650 0 4 _aBrain
_xenzymology
650 0 4 _aBrain Edema
_xetiology
650 0 4 _aCalcium Compounds
650 0 4 _aCanavan Disease
_xdiagnosis
650 0 4 _aChild
650 0 4 _aChild, Preschool
650 0 4 _aCholesterol
_xadministration & dosage
650 0 4 _aCombined Modality Therapy
650 0 4 _aCytomegalovirus
_xgenetics
650 0 4 _aDNA, Recombinant
_xadministration & dosage
650 0 4 _aDependovirus
_xgenetics
650 0 4 _aFemale
650 0 4 _aFetal Diseases
_xdiagnosis
650 0 4 _aGenetic Therapy
650 0 4 _aGenetic Vectors
_xadministration & dosage
650 0 4 _aGlycerophospholipids
_xadministration & dosage
650 0 4 _aHumans
650 0 4 _aInfant
650 0 4 _aInjections, Intraventricular
650 0 4 _aLiposomes
_xadministration & dosage
650 0 4 _aMale
650 0 4 _aMitochondria
_xmetabolism
650 0 4 _aNerve Tissue Proteins
_xdeficiency
650 0 4 _aOsmotic Pressure
650 0 4 _aPhosphatidylethanolamines
650 0 4 _aPrenatal Diagnosis
650 0 4 _aPrimates
650 0 4 _aPromoter Regions, Genetic
650 0 4 _aProtamines
_xadministration & dosage
650 0 4 _aRats
700 1 _aJanson, C G
700 1 _aMcPhee, S J
700 1 _aDuring, M J
773 0 _tCurrent opinion in molecular therapeutics
_gvol. 1
_gno. 4
_gp. 487-92
999 _c11628378
_d11628378