The long-term safety and efficacy of vestronidase alfa, rhGUS enzyme replacement therapy, in subjects with mucopolysaccharidosis VII. [electronic resource]
Producer: 20201123Description: 219-227 p. digitalISSN:- 1096-7206
- Adolescent
- Adult
- Antibodies, Neutralizing
- Blood-Brain Barrier -- drug effects
- Child
- Cross-Over Studies
- Enzyme Replacement Therapy
- Female
- Glucuronidase -- administration & dosage
- Glycosaminoglycans -- urine
- Humans
- Male
- Mucopolysaccharidosis VII -- drug therapy
- Rare Diseases -- therapy
- Treatment Outcome
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Publication Type: Clinical Trial, Phase III; Journal Article; Randomized Controlled Trial; Research Support, Non-U.S. Gov't
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