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Demonstrating significant benefit of orphan medicines: analysis of 15 years of experience in Europe. [electronic resource] by
- Fregonese, Laura
- Greene, Lesley
- Hofer, Matthias
- Magrelli, Armando
- Naumann-Winter, Frauke
- Larsson, Kristina
- Sheean, Maria
- Stoyanova-Beninska, Violeta
- Tsigkos, Stelios
- Westermark, Kerstin
- Sepodes, Bruno
Producer: 20181015
In:
Drug discovery today vol. 23
Availability: No items available.
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11.
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Use of biomarkers in the context of orphan medicines designation in the European Union. [electronic resource] by
- Tsigkos, Stelios
- Llinares, Jordi
- Mariz, Segundo
- Aarum, Stiina
- Fregonese, Laura
- Dembowska-Baginska, Bozenna
- Elbers, Rembert
- Evers, Pauline
- Foltanova, Tatiana
- Lhoir, Andre
- Corrêa-Nunes, Ana
- O'Connor, Daniel
- Voordouw, Albertha
- Westermark, Kerstin
- Sepodes, Bruno
Producer: 20140926
In:
Orphanet journal of rare diseases vol. 9
Availability: No items available.
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12.
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Defining orphan conditions in the context of the European orphan regulation: challenges and evolution. [electronic resource] by
- O'Connor, Daniel J
- Sheean, Maria E
- Hofer, Matthias P
- Tsigkos, Stelios
- Mariz, Segundo
- Fregonese, Laura
- Larsson, Kristina
- Hivert, Virginie
- Westermark, Kerstin
- Naumann-Winter, Frauke
- Stoyanova-Beninska, Violeta
- Barišić, Ingeborg
- Capovilla, Giuseppe
- Magrelli, Armando
- Sepodes, Bruno
Producer: 20200131
In:
Nature reviews. Drug discovery vol. 18
Availability: No items available.
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13.
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European regulation on orphan medicinal products: 10 years of experience and future perspectives. [electronic resource] by
- Westermark, Kerstin
- Holm, Birthe Byskov
- Söderholm, Mirjam
- Llinares-Garcia, Jordi
- Rivière, Frida
- Aarum, Stiina
- Butlen-Ducuing, Florence
- Tsigkos, Stelios
- Wilk-Kachlicka, Agnieszka
- N'Diamoi, Cinzia
- Borvendég, János
- Lyons, David
- Sepodes, Bruno
- Bloechl-Daum, Brigitte
- Lhoir, André
- Todorova, Mariana
- Kkolos, Ioannis
- Kubáčková, Kateřina
- Bosch-Traberg, Heidrun
- Tillmann, Vallo
- Saano, Veijo
- Héron, Emmanuel
- Elbers, Rembert
- Siouti, Miranda
- Eggenhofer, Judit
- Salmon, Patrick
- Clementi, Maurizio
- Krieviņš, Dainis
- Matulevičiene, Aušra
- Metz, Henri
- Vincenti, Albert Cilia
- Voordouw, Albertha
- Dembowska-Bagińska, Bożenna
- Nunes, Ana Corrêa
- Saleh, Flavia Mirela
- Foltánová, Tatiana
- Možina, Martin
- Torrent i Farnell, Josep
- Beerman, Björn
- Mariz, Segundo
- Evers, Marie Pauline
- Greene, Lesley
- Thorsteinsson, Sigurdur
- Gramstad, Lars
- Mavris, Maria
- Bignami, Fabrizia
- Lorence, Annie
- Belorgey, Chantal
Producer: 20110701
In:
Nature reviews. Drug discovery vol. 10
Availability: No items available.
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