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Intrathecal Adeno-Associated Viral Vector-Mediated Gene Delivery for Adrenomyeloneuropathy. [electronic resource] by
- Gong, Yi
- Berenson, Anna
- Laheji, Fiza
- Gao, Guangping
- Wang, Dan
- Ng, Carrie
- Volak, Adrienn
- Kok, Rene
- Kreouzis, Vasileios
- Dijkstra, Inge M
- Kemp, Stephan
- Maguire, Casey A
- Eichler, Florian
Producer: 20200312
In:
Human gene therapy vol. 30
Availability: No items available.
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CRISPR/Cas9 Mediated Disruption of the Swedish APP Allele as a Therapeutic Approach for Early-Onset Alzheimer's Disease. [electronic resource] by
- György, Bence
- Lööv, Camilla
- Zaborowski, Mikołaj P
- Takeda, Shuko
- Kleinstiver, Benjamin P
- Commins, Caitlin
- Kastanenka, Ksenia
- Mu, Dakai
- Volak, Adrienn
- Giedraitis, Vilmantas
- Lannfelt, Lars
- Maguire, Casey A
- Joung, J Keith
- Hyman, Bradley T
- Breakefield, Xandra O
- Ingelsson, Martin
Publication details: Molecular therapy. Nucleic acids Jun 2018
In:
Molecular therapy. Nucleic acids vol. 11
Availability: No items available.
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5.
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Rescue of Hearing by Gene Delivery to Inner-Ear Hair Cells Using Exosome-Associated AAV. [electronic resource] by
- György, Bence
- Sage, Cyrille
- Indzhykulian, Artur A
- Scheffer, Deborah I
- Brisson, Alain R
- Tan, Sisareuth
- Wu, Xudong
- Volak, Adrienn
- Mu, Dakai
- Tamvakologos, Panos I
- Li, Yaqiao
- Fitzpatrick, Zachary
- Ericsson, Maria
- Breakefield, Xandra O
- Corey, David P
- Maguire, Casey A
Producer: 20170606
In:
Molecular therapy : the journal of the American Society of Gene Therapy vol. 25
Availability: No items available.
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Virus vector-mediated genetic modification of brain tumor stromal cells after intravenous delivery. [electronic resource] by
- Volak, Adrienn
- LeRoy, Stanley G
- Natasan, Jeya Shree
- Park, David J
- Cheah, Pike See
- Maus, Andreas
- Fitzpatrick, Zachary
- Hudry, Eloise
- Pinkham, Kelsey
- Gandhi, Sheetal
- Hyman, Bradley T
- Mu, Dakai
- GuhaSarkar, Dwijit
- Stemmer-Rachamimov, Anat O
- Sena-Esteves, Miguel
- Badr, Christian E
- Maguire, Casey A
Producer: 20190809
In:
Journal of neuro-oncology vol. 139
Availability: No items available.
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Gene Transfer with AAV9-PHP.B Rescues Hearing in a Mouse Model of Usher Syndrome 3A and Transduces Hair Cells in a Non-human Primate. [electronic resource] by
- György, Bence
- Meijer, Elise J
- Ivanchenko, Maryna V
- Tenneson, Kelly
- Emond, Frederick
- Hanlon, Killian S
- Indzhykulian, Artur A
- Volak, Adrienn
- Karavitaki, K Domenica
- Tamvakologos, Panos I
- Vezina, Mark
- Berezovskii, Vladimir K
- Born, Richard T
- O'Brien, Maureen
- Lafond, Jean-François
- Arsenijevic, Yvan
- Kenna, Margaret A
- Maguire, Casey A
- Corey, David P
Publication details: Molecular therapy. Methods & clinical development Jun 2019
In:
Molecular therapy. Methods & clinical development vol. 13
Availability: No items available.
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High levels of AAV vector integration into CRISPR-induced DNA breaks. [electronic resource] by
- Hanlon, Killian S
- Kleinstiver, Benjamin P
- Garcia, Sara P
- Zaborowski, Mikołaj P
- Volak, Adrienn
- Spirig, Stefan E
- Muller, Alissa
- Sousa, Alexander A
- Tsai, Shengdar Q
- Bengtsson, Niclas E
- Lööv, Camilla
- Ingelsson, Martin
- Chamberlain, Jeffrey S
- Corey, David P
- Aryee, Martin J
- Joung, J Keith
- Breakefield, Xandra O
- Maguire, Casey A
- György, Bence
Producer: 20200106
In:
Nature communications vol. 10
Availability: No items available.
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