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Authors
- 't Hoen, Peter A C
- Aartsma-Rus, Annemieke
- Aartsma-Rus, Annemieke M
- Aguilera, Begona
- Andersen, Jan Terje
- Anthony, Karen
- Arechavala-Gomeza, Virginia
- Bjarnarson, Stefania P
- Bosgra, Sieto
- Datson, Nicole A
- Diaz Parillas, Valeriano
- Dickson, George
- Falzarano, Maria Sofia
- Ferlini, Alessandra
- Garcia-Jimenez, Iker
- Gerritsen, Jacoline
- Goeman, Jelle J
- González-Barriga, Anchel
- Verheul, Ruurd C
- van Deutekom, Judith C T
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Topics
- Agammaglobulinemia
- Alternative Splicing
- Amino Acid Sequence
- Amino Acid Substitution
- Animals
- Antibodies, Monoclonal
- Arginine
- Binding, Competitive
- Cell Line
- Disease Models, Animal
- Dystrophin
- Exons
- Humans
- Mice
- Muscular Dystrophy, Duchenne
- Oligonucleotides, Antisense
- Polymerase Chain Reaction
- administration & dosage
- genetics
- methods
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