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The Gene Therapy Resource Program: A Decade of Dedication to Translational Research by the National Heart, Lung, and Blood Institute. [electronic resource] by
- Flotte, Terence R
- Daniels, Eric
- Benson, Janet
- Bevett-Rose, Jeneé M
- Cornetta, Kenneth
- Diggins, Margaret
- Johnston, Julie
- Sepelak, Susan
- van der Loo, Johannes C M
- Wilson, James M
- McDonald, Cheryl L
Producer: 20180730
In:
Human gene therapy. Clinical development vol. 28
Availability: No items available.
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8.
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Production and purification of high-titer foamy virus vector for the treatment of leukocyte adhesion deficiency. [electronic resource] by
- Nasimuzzaman, Md
- Lynn, Danielle
- Ernst, Rebecca
- Beuerlein, Michele
- Smith, Richard H
- Shrestha, Archana
- Cross, Scott
- Link, Kevin
- Lutzko, Carolyn
- Nordling, Diana
- Russell, David W
- Larochelle, Andre
- Malik, Punam
- Van der Loo, Johannes C M
Publication details: Molecular therapy. Methods & clinical development 2016
In:
Molecular therapy. Methods & clinical development vol. 3
Availability: No items available.
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9.
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Familial pulmonary alveolar proteinosis caused by mutations in CSF2RA. [electronic resource] by
- Suzuki, Takuji
- Sakagami, Takuro
- Rubin, Bruce K
- Nogee, Lawrence M
- Wood, Robert E
- Zimmerman, Sarah L
- Smolarek, Teresa
- Dishop, Megan K
- Wert, Susan E
- Whitsett, Jeffrey A
- Grabowski, Gregory
- Carey, Brenna C
- Stevens, Carrie
- van der Loo, Johannes C M
- Trapnell, Bruce C
Producer: 20081229
In:
The Journal of experimental medicine vol. 205
Availability: No items available.
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10.
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Hemophilia B Gene Therapy with a High-Specific-Activity Factor IX Variant. [electronic resource] by
- George, Lindsey A
- Sullivan, Spencer K
- Giermasz, Adam
- Rasko, John E J
- Samelson-Jones, Benjamin J
- Ducore, Jonathan
- Cuker, Adam
- Sullivan, Lisa M
- Majumdar, Suvankar
- Teitel, Jerome
- McGuinn, Catherine E
- Ragni, Margaret V
- Luk, Alvin Y
- Hui, Daniel
- Wright, J Fraser
- Chen, Yifeng
- Liu, Yun
- Wachtel, Katie
- Winters, Angela
- Tiefenbacher, Stefan
- Arruda, Valder R
- van der Loo, Johannes C M
- Zelenaia, Olga
- Takefman, Daniel
- Carr, Marcus E
- Couto, Linda B
- Anguela, Xavier M
- High, Katherine A
Producer: 20171215
In:
The New England journal of medicine vol. 377
Availability: No items available.
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11.
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A modified γ-retrovirus vector for X-linked severe combined immunodeficiency. [electronic resource] by
- Hacein-Bey-Abina, Salima
- Pai, Sung-Yun
- Gaspar, H Bobby
- Armant, Myriam
- Berry, Charles C
- Blanche, Stephane
- Bleesing, Jack
- Blondeau, Johanna
- de Boer, Helen
- Buckland, Karen F
- Caccavelli, Laure
- Cros, Guilhem
- De Oliveira, Satiro
- Fernández, Karen S
- Guo, Dongjing
- Harris, Chad E
- Hopkins, Gregory
- Lehmann, Leslie E
- Lim, Annick
- London, Wendy B
- van der Loo, Johannes C M
- Malani, Nirav
- Male, Frances
- Malik, Punam
- Marinovic, M Angélica
- McNicol, Anne-Marie
- Moshous, Despina
- Neven, Benedicte
- Oleastro, Matías
- Picard, Capucine
- Ritz, Jerome
- Rivat, Christine
- Schambach, Axel
- Shaw, Kit L
- Sherman, Eric A
- Silberstein, Leslie E
- Six, Emmanuelle
- Touzot, Fabien
- Tsytsykova, Alla
- Xu-Bayford, Jinhua
- Baum, Christopher
- Bushman, Frederic D
- Fischer, Alain
- Kohn, Donald B
- Filipovich, Alexandra H
- Notarangelo, Luigi D
- Cavazzana, Marina
- Williams, David A
- Thrasher, Adrian J
Producer: 20141022
In:
The New England journal of medicine vol. 371
Availability: No items available.
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