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Adult care for Duchenne muscular dystrophy in the UK. [electronic resource] by
- Rodger, Sunil
- Woods, Katherine L
- Bladen, Catherine L
- Stringer, Angela
- Vry, Julia
- Gramsch, Kathrin
- Kirschner, Janbernd
- Thompson, Rachel
- Bushby, Katharine
- Lochmüller, Hanns
Producer: 20160229
In:
Journal of neurology vol. 262
Availability: No items available.
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The TREAT-NMD DMD Global Database: analysis of more than 7,000 Duchenne muscular dystrophy mutations. [electronic resource] by
- Bladen, Catherine L
- Salgado, David
- Monges, Soledad
- Foncuberta, Maria E
- Kekou, Kyriaki
- Kosma, Konstantina
- Dawkins, Hugh
- Lamont, Leanne
- Roy, Anna J
- Chamova, Teodora
- Guergueltcheva, Velina
- Chan, Sophelia
- Korngut, Lawrence
- Campbell, Craig
- Dai, Yi
- Wang, Jen
- Barišić, Nina
- Brabec, Petr
- Lahdetie, Jaana
- Walter, Maggie C
- Schreiber-Katz, Olivia
- Karcagi, Veronika
- Garami, Marta
- Viswanathan, Venkatarman
- Bayat, Farhad
- Buccella, Filippo
- Kimura, En
- Koeks, Zaïda
- van den Bergen, Janneke C
- Rodrigues, Miriam
- Roxburgh, Richard
- Lusakowska, Anna
- Kostera-Pruszczyk, Anna
- Zimowski, Janusz
- Santos, Rosário
- Neagu, Elena
- Artemieva, Svetlana
- Rasic, Vedrana Milic
- Vojinovic, Dina
- Posada, Manuel
- Bloetzer, Clemens
- Jeannet, Pierre-Yves
- Joncourt, Franziska
- Díaz-Manera, Jordi
- Gallardo, Eduard
- Karaduman, A Ayşe
- Topaloğlu, Haluk
- El Sherif, Rasha
- Stringer, Angela
- Shatillo, Andriy V
- Martin, Ann S
- Peay, Holly L
- Bellgard, Matthew I
- Kirschner, Jan
- Flanigan, Kevin M
- Straub, Volker
- Bushby, Kate
- Verschuuren, Jan
- Aartsma-Rus, Annemieke
- Béroud, Christophe
- Lochmüller, Hanns
Producer: 20151217
In:
Human mutation vol. 36
Availability: No items available.
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The TREAT-NMD Duchenne muscular dystrophy registries: conception, design, and utilization by industry and academia. [electronic resource] by
- Bladen, Catherine L
- Rafferty, Karen
- Straub, Volker
- Monges, Soledad
- Moresco, Angélica
- Dawkins, Hugh
- Roy, Anna
- Chamova, Teodora
- Guergueltcheva, Velina
- Korngut, Lawrence
- Campbell, Craig
- Dai, Yi
- Barišić, Nina
- Kos, Tea
- Brabec, Petr
- Rahbek, Jes
- Lahdetie, Jaana
- Tuffery-Giraud, Sylvie
- Claustres, Mireille
- Leturcq, France
- Ben Yaou, Rabah
- Walter, Maggie C
- Schreiber, Olivia
- Karcagi, Veronika
- Herczegfalvi, Agnes
- Viswanathan, Venkatarman
- Bayat, Farhad
- de la Caridad Guerrero Sarmiento, Isis
- Ambrosini, Anna
- Ceradini, Francesca
- Kimura, En
- van den Bergen, Janneke C
- Rodrigues, Miriam
- Roxburgh, Richard
- Lusakowska, Anna
- Oliveira, Jorge
- Santos, Rosário
- Neagu, Elena
- Butoianu, Niculina
- Artemieva, Svetlana
- Rasic, Vedrana Milic
- Posada, Manuel
- Palau, Francesc
- Lindvall, Björn
- Bloetzer, Clemens
- Karaduman, Ayşe
- Topaloğlu, Haluk
- Inal, Serap
- Oflazer, Piraye
- Stringer, Angela
- Shatillo, Andriy V
- Martin, Ann S
- Peay, Holly
- Flanigan, Kevin M
- Salgado, David
- von Rekowski, Brigitta
- Lynn, Stephen
- Heslop, Emma
- Gainotti, Sabina
- Taruscio, Domenica
- Kirschner, Jan
- Verschuuren, Jan
- Bushby, Kate
- Béroud, Christophe
- Lochmüller, Hanns
Producer: 20140508
In:
Human mutation vol. 34
Availability: No items available.
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Clinical Outcomes in Duchenne Muscular Dystrophy: A Study of 5345 Patients from the TREAT-NMD DMD Global Database. [electronic resource] by
- Koeks, Zaïda
- Bladen, Catherine L
- Salgado, David
- van Zwet, Erik
- Pogoryelova, Oksana
- McMacken, Grace
- Monges, Soledad
- Foncuberta, Maria E
- Kekou, Kyriaki
- Kosma, Konstantina
- Dawkins, Hugh
- Lamont, Leanne
- Bellgard, Matthew I
- Roy, Anna J
- Chamova, Teodora
- Guergueltcheva, Velina
- Chan, Sophelia
- Korngut, Lawrence
- Campbell, Craig
- Dai, Yi
- Wang, Jen
- Barišić, Nina
- Brabec, Petr
- Lähdetie, Jaana
- Walter, Maggie C
- Schreiber-Katz, Olivia
- Karcagi, Veronika
- Garami, Marta
- Herczegfalvi, Agnes
- Viswanathan, Venkatarman
- Bayat, Farhad
- Buccella, Filippo
- Ferlini, Alessandra
- Kimura, En
- van den Bergen, Janneke C
- Rodrigues, Miriam
- Roxburgh, Richard
- Lusakowska, Anna
- Kostera-Pruszczyk, Anna
- Santos, Rosário
- Neagu, Elena
- Artemieva, Svetlana
- Rasic, Vedrana Milic
- Vojinovic, Dina
- Posada, Manuel
- Bloetzer, Clemens
- Klein, Andrea
- Díaz-Manera, Jordi
- Gallardo, Eduard
- Karaduman, A Ayşe
- Oznur, Tunca
- Topaloğlu, Haluk
- El Sherif, Rasha
- Stringer, Angela
- Shatillo, Andriy V
- Martin, Ann S
- Peay, Holly L
- Kirschner, Jan
- Flanigan, Kevin M
- Straub, Volker
- Bushby, Kate
- Béroud, Christophe
- Verschuuren, Jan J
- Lochmüller, Hanns
Producer: 20190702
In:
Journal of neuromuscular diseases vol. 4
Availability: No items available.
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