Results
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1.
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Bioengineered constructs combined with exercise enhance stem cell-mediated treatment of volumetric muscle loss. [electronic resource] by
- Quarta, Marco
- Cromie, Melinda
- Chacon, Robert
- Blonigan, Justin
- Garcia, Victor
- Akimenko, Igor
- Hamer, Mark
- Paine, Patrick
- Stok, Merel
- Shrager, Joseph B
- Rando, Thomas A
Producer: 20181119
In:
Nature communications vol. 8
Availability: No items available.
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2.
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Lentiviral Stem Cell Gene Therapy for Pompe Disease. [electronic resource] by
- Liang, Qiushi
- Stok, Merel
- van Helsdingen, Yvette
- van der Velden, Guus
- Jacobs, Ed
- Duncker, Dirk
- Reuser, Arnold
- van der Ploeg, Ans
- Vulto, Arnold
- van Til, Niek P
- Wagemaker, Gerard
Publication details: Journal of neuromuscular diseases
In:
Journal of neuromuscular diseases vol. 2
Availability: No items available.
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3.
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Pompe disease in adulthood: effects of antibody formation on enzyme replacement therapy. [electronic resource] by
- de Vries, Juna M
- Kuperus, Esther
- Hoogeveen-Westerveld, Marianne
- Kroos, Marian A
- Wens, Stephan C A
- Stok, Merel
- van der Beek, Nadine A M E
- Kruijshaar, Michelle E
- Rizopoulos, Dimitris
- van Doorn, Pieter A
- van der Ploeg, Ans T
- Pijnappel, W W M Pim
Producer: 20171207
In:
Genetics in medicine : official journal of the American College of Medical Genetics vol. 19
Availability: No items available.
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4.
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Response to Herbert et al. [electronic resource] by
- de Vries, Juna M
- Kuperus, Esther
- Hoogeveen-Westerveld, Marianne
- Kroos, Marian A
- Wens, Stephan C A
- Stok, Merel
- van der Beek, Nadine A M E
- Kruijshaar, Michelle E
- Rizopoulos, Dimitris
- van Doorn, Pieter A
- van der Ploeg, Ans T
- Pijnappel, W W M Pim
Producer: 20180605
In:
Genetics in medicine : official journal of the American College of Medical Genetics vol. 19
Availability: No items available.
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5.
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Gene therapy augments the efficacy of hematopoietic cell transplantation and fully corrects mucopolysaccharidosis type I phenotype in the mouse model. [electronic resource] by
- Visigalli, Ilaria
- Delai, Stefania
- Politi, Letterio S
- Di Domenico, Carmela
- Cerri, Federica
- Mrak, Emanuela
- D'Isa, Raffaele
- Ungaro, Daniela
- Stok, Merel
- Sanvito, Francesca
- Mariani, Elisabetta
- Staszewsky, Lidia
- Godi, Claudia
- Russo, Ilaria
- Cecere, Francesca
- Del Carro, Ubaldo
- Rubinacci, Alessandro
- Brambilla, Riccardo
- Quattrini, Angelo
- Di Natale, Paola
- Ponder, Katherine
- Naldini, Luigi
- Biffi, Alessandra
Producer: 20110106
In:
Blood vol. 116
Availability: No items available.
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6.
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Preclinical Efficacy and Safety Evaluation of Hematopoietic Stem Cell Gene Therapy in a Mouse Model of MNGIE. [electronic resource] by
- Yadak, Rana
- Cabrera-Pérez, Raquel
- Torres-Torronteras, Javier
- Bugiani, Marianna
- Haeck, Joost C
- Huston, Marshall W
- Bogaerts, Elly
- Goffart, Steffi
- Jacobs, Edwin H
- Stok, Merel
- Leonardelli, Lorena
- Biasco, Luca
- Verdijk, Robert M
- Bernsen, Monique R
- Ruijter, George
- Martí, Ramon
- Wagemaker, Gerard
- van Til, Niek P
- de Coo, Irenaeus F M
Publication details: Molecular therapy. Methods & clinical development Mar 2018
In:
Molecular therapy. Methods & clinical development vol. 8
Availability: No items available.
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7.
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Lentiviral gene therapy of murine hematopoietic stem cells ameliorates the Pompe disease phenotype. [electronic resource] by
- van Til, Niek P
- Stok, Merel
- Aerts Kaya, Fatima S F
- de Waard, Monique C
- Farahbakhshian, Elnaz
- Visser, Trudi P
- Kroos, Marian A
- Jacobs, Edwin H
- Willart, Monique A
- van der Wegen, Pascal
- Scholte, Bob J
- Lambrecht, Bart N
- Duncker, Dirk J
- van der Ploeg, Ans T
- Reuser, Arnold J J
- Verstegen, Monique M
- Wagemaker, Gerard
Producer: 20100802
In:
Blood vol. 115
Availability: No items available.
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